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Safety and Efficacy of Omaveloxolone in Friedreich Ataxia (MOXIe Study).
Lynch, David R; Chin, Melanie P; Delatycki, Martin B; Subramony, S H; Corti, Manuela; Hoyle, J Chad; Boesch, Sylvia; Nachbauer, Wolfgang; Mariotti, Caterina; Mathews, Katherine D; Giunti, Paola; Wilmot, George; Zesiewicz, Theresa; Perlman, Susan; Goldsberry, Angie; O'Grady, Megan; Meyer, Colin J.
Afiliação
  • Lynch DR; Division of Neurology, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Chin MP; Reata Pharmaceuticals, Dallas, TX, USA.
  • Delatycki MB; Victorian Clinical Genetics Services, Murdoch Children's Research Institute, Parkville, Victoria, Australia.
  • Subramony SH; Department of Neurology, McKnight Brain Institute, University of Florida Health System, Gainesville, FL, USA.
  • Corti M; Department of Pediatrics, University of Florida Health System, Gainesville, FL, USA.
  • Hoyle JC; Department of Neurology, Ohio State University College of Medicine, Columbus, OH, USA.
  • Boesch S; Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
  • Nachbauer W; Department of Neurology, Medical University Innsbruck, Innsbruck, Austria.
  • Mariotti C; Istituto di Ricovero e Cura a Carattere Scientifico-Carlo Besta Neurological Institute, Milan, Italy.
  • Mathews KD; Department of Neurology, University of Iowa Carver College of Medicine, Iowa City, IA, USA.
  • Giunti P; University College London Hospital, London, United Kingdom.
  • Wilmot G; Department of Neurology, Emory University School of Medicine, Atlanta, GA, USA.
  • Zesiewicz T; Department of Neurology, University of South Florida Ataxia Research Center, Tampa, FL, USA.
  • Perlman S; Department of Neurology, University of California, Los Angeles, Los Angeles, CA, USA.
  • Goldsberry A; Reata Pharmaceuticals, Dallas, TX, USA.
  • O'Grady M; Reata Pharmaceuticals, Dallas, TX, USA.
  • Meyer CJ; Reata Pharmaceuticals, Dallas, TX, USA.
Ann Neurol ; 89(2): 212-225, 2021 02.
Article em En | MEDLINE | ID: mdl-33068037

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Triterpenos / Ataxia de Friedreich Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male Idioma: En Revista: Ann Neurol Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Triterpenos / Ataxia de Friedreich Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adolescent / Adult / Female / Humans / Male Idioma: En Revista: Ann Neurol Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos