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Natural history study of factor IX deficiency with focus on treatment and complications (B-Natural).
Shapiro, Amy D; Ragni, Margaret V; Borhany, Munira; Abajas, Yasmina L; Tarantino, Michael D; Holstein, Katharina; Croteau, Stacy E; Liesner, Riana; Tarango, Cristina; Carvalho, Manuela; McGuinn, Catherine; Funding, Eva; Kempton, Christine L; Bidlingmaier, Christoph; Cohen, Alice; Oldenburg, Johannes; Kearney, Susan; Knoll, Christine; Kuriakose, Philip; Acharya, Suchitra; Reiss, Ulrike M; Kulkarni, Roshni; Witkop, Michelle; Lethagen, Stefan; Donfield, Sharyne; LeBeau, Petra; Berntorp, Erik; Astermark, Jan.
Afiliação
  • Shapiro AD; Indiana Hemophilia and Thrombosis Center, Indianapolis, IN, USA.
  • Ragni MV; Hemophilia Center of Western Pennsylvania, University of Pittsburgh, Pittsburgh, PA, USA.
  • Borhany M; National Institute of Blood Disease and Bone Marrow Transplantation, Karachi, Pakistan.
  • Abajas YL; Hemophilia and Thrombosis Center, University of North Carolina, Chapel Hill, NC, USA.
  • Tarantino MD; Bleeding and Clotting Disorders Institute, Peoria, IL, USA.
  • Holstein K; Medical Department, Haemophilia Center, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Croteau SE; Boston Hemophilia Center, Boston Children's Hospital, Boston, MA, USA.
  • Liesner R; Great Ormond Street Hospital for Children, NHS Trust supported by NIHR, GOSH, BRC, London, UK.
  • Tarango C; Department of Pediatrics, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Carvalho M; Congenital Coagulopathies Reference Centre, Centro Hospitalar Universitário São João, Porto, Portugal.
  • McGuinn C; Weill Cornell Medical College, New York, NY, USA.
  • Funding E; Department of Hematology, University Hospital Rigshospitalet, Institute of Clinical Medicine, University of Copenhagen, Copenhagen, Denmark.
  • Kempton CL; Emory University School of Medicine, Emory University, Atlanta, GA, USA.
  • Bidlingmaier C; Dr. v. Hauner's Childrens University Hospital, Hemophilia Center, LMU Hospital, Munich, Germany.
  • Cohen A; Newark Beth Israel Medical Center, Newark, NJ, USA.
  • Oldenburg J; University Clinic Bonn, Bonn, Germany.
  • Kearney S; Children's Minnesota Center for Bleeding and Clotting Disorders, Minneapolis, MN, USA.
  • Knoll C; Phoenix Children's Hospital, Phoenix, AZ, USA.
  • Kuriakose P; Henry Ford Hospital, Detroit, MI, USA.
  • Acharya S; Northwell Hemostasis and Thrombosis Center, New York, NY, USA.
  • Reiss UM; St. Jude Children's Research Hospital, Memphis, TN, USA.
  • Kulkarni R; Michigan State University, East Lansing, MI, USA.
  • Witkop M; Northern Regional Bleeding Disorders Center, Munson Medical Center, Traverse City, MI, USA.
  • Lethagen S; Sobi, Stockholm, Sweden.
  • Donfield S; Rho, Inc., Durham, NC, USA.
  • LeBeau P; Rho, Inc., Durham, NC, USA.
  • Berntorp E; Clinical Coagulation Research, Department of Translational Medicine, Lund University, Malmö, Sweden.
  • Astermark J; Department of Translational Medicine, Lund University, Malmö, Sweden.
Haemophilia ; 27(1): 49-59, 2021 Jan.
Article em En | MEDLINE | ID: mdl-33278853

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemofilia B / Hemofilia A Tipo de estudo: Observational_studies Limite: Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemofilia B / Hemofilia A Tipo de estudo: Observational_studies Limite: Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Estados Unidos