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Curative Treatment of POMP-Related Autoinflammation and Immune Dysregulation (PRAID) by Hematopoietic Stem Cell Transplantation.
Meinhardt, Andrea; Ramos, Paula C; Dohmen, R Jürgen; Lucas, Nadja; Lee-Kirsch, Min Ae; Becker, Benjamin; de Laffolie, Jan; Cunha, Tomás; Niehues, Tim; Salzer, Ulrich; Yoshimi, Ayami; Erlacher, Miriam; Peters, Anke M J; Ehl, Stephan; Strahm, Brigitte; Speckmann, Carsten.
Afiliação
  • Meinhardt A; Center for Pediatrics and Adolescent Medicine, Medical Center, University Hospital Giessen, Giessen, Germany.
  • Ramos PC; Institute for Genetics, Center of Molecular Biosciences, Department of Biology, Faculty of Mathematics and Natural Sciences, University of Cologne, Cologne, Germany.
  • Dohmen RJ; Institute for Genetics, Center of Molecular Biosciences, Department of Biology, Faculty of Mathematics and Natural Sciences, University of Cologne, Cologne, Germany.
  • Lucas N; Department of Pediatrics, Medical Faculty and University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
  • Lee-Kirsch MA; Department of Pediatrics, Medical Faculty and University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
  • Becker B; Center for Pediatrics and Adolescent Medicine, Medical Center, University Hospital Giessen, Giessen, Germany.
  • de Laffolie J; Center for Pediatrics and Adolescent Medicine, Medical Center, University Hospital Giessen, Giessen, Germany.
  • Cunha T; Center for Dermatology and Allergology, Medical Center, University Hospital Marburg, Marburg, Germany.
  • Niehues T; Center for Pediatrics and Adolescent Medicine, Helios Hospital Krefeld, Krefeld, Germany.
  • Salzer U; Institute for Immunodeficiency, Center for Chronic Immunodeficiency (CCI), Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Yoshimi A; Center for Pediatrics and Adolescent Medicine, Department of Pediatric Hematology and Oncology, Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Erlacher M; Center for Pediatrics and Adolescent Medicine, Department of Pediatric Hematology and Oncology, Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Peters AMJ; Center for Pediatrics and Adolescent Medicine, Department of Pediatric Hematology and Oncology, Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Ehl S; Institute for Immunodeficiency, Center for Chronic Immunodeficiency (CCI), Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Strahm B; Center for Pediatrics and Adolescent Medicine, Department of Pediatric Hematology and Oncology, Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany.
  • Speckmann C; Institute for Immunodeficiency, Center for Chronic Immunodeficiency (CCI), Faculty of Medicine, Medical Center-University of Freiburg, Freiburg, Germany. carsten.speckmann@uniklinik-freiburg.de.
J Clin Immunol ; 41(7): 1664-1667, 2021 10.
Article em En | MEDLINE | ID: mdl-34131834

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Chaperonas Moleculares / Transplante de Células-Tronco Hematopoéticas / Síndromes de Imunodeficiência Limite: Humans / Infant / Male Idioma: En Revista: J Clin Immunol Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Chaperonas Moleculares / Transplante de Células-Tronco Hematopoéticas / Síndromes de Imunodeficiência Limite: Humans / Infant / Male Idioma: En Revista: J Clin Immunol Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Alemanha