Your browser doesn't support javascript.
loading
Efficacy and safety of givosiran for acute hepatic porphyria: 24-month interim analysis of the randomized phase 3 ENVISION study.
Ventura, Paolo; Bonkovsky, Herbert L; Gouya, Laurent; Aguilera-Peiró, Paula; Montgomery Bissell, D; Stein, Penelope E; Balwani, Manisha; Anderson, D Karl E; Parker, Charles; Kuter, David J; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J; Hua, Zhaowei; Sweetser, Marianne T; Sardh, Eliane.
Afiliação
  • Ventura P; Department of Surgical and Medical Sciences for Children and Adults, Internal Medicine Unit, University of Modena and Reggio Emilia, Modena, Italy.
  • Bonkovsky HL; Section on Gastroenterology and Hepatology, Wake Forest University/North Carolina Baptist Medical Center, Winston-Salem, NC, USA.
  • Gouya L; Centre Français des Porphyries, Paris, France.
  • Aguilera-Peiró P; Hospital Clinic Barcelona, Barcelona, Spain.
  • Montgomery Bissell D; UCSF Liver Center and Porphyria Center, University of California, San Francisco, CA, USA.
  • Stein PE; King's College Hospital, London, UK.
  • Balwani M; Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, USA.
  • Anderson DKE; University of Texas Medical Branch, Galveston, TX, USA.
  • Parker C; University of Utah, Salt Lake City, UT, USA.
  • Kuter DJ; Center for Hematology, Massachusetts General Hospital, Boston, MA, USA.
  • Monroy S; Instituto Nacional de Pediatría, Mexico City, Mexico.
  • Oh J; Konkuk University Medical Center, Seoul, South Korea.
  • Ritchie B; University of Alberta Hospital, Edmonton, Canada.
  • Ko JJ; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Hua Z; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Sweetser MT; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Sardh E; Porphyria Centre Sweden, Centre for Inherited Metabolic Diseases, Karolinska Institutet, Karolinska University Hospital, Stockholm, Sweden.
Liver Int ; 42(1): 161-172, 2022 01.
Article em En | MEDLINE | ID: mdl-34717041

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Porfirias Hepáticas / Porfiria Aguda Intermitente Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Revista: Liver Int Assunto da revista: GASTROENTEROLOGIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Porfirias Hepáticas / Porfiria Aguda Intermitente Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Revista: Liver Int Assunto da revista: GASTROENTEROLOGIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália