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Respiratory management of spinal muscular atrophy type 1 patients treated with Nusinersen.
Menard, Joris; Seferian, Andreea M; Fleurence, Emmanuelle; Barzic, Audrey; Binoche, Alexandra; Labouret, Géraldine; Coutier, Laurianne; Vuillerot, Carole; Bieleu, Blaise M; Gomez Garcia de la Banda, Marta; Corvol, Harriet; Servais, Laurent; Taytard, Jessica.
Afiliação
  • Menard J; Department of Pediatric Pulmonology, Armand Trousseau University Hospital, Paris, France.
  • Seferian AM; I-Motion, Hôpital Armand Trousseau, Paris, France.
  • Fleurence E; ESEAN-APF, Health Center for Children and Adolescents, Nantes, France.
  • Barzic A; Department of Pediatric, Fondation Ildys, Brest, France.
  • Binoche A; Pediatric Intensive Care Unit Department, Centre Hospitalier Universitaire de Lille, Lille, France.
  • Labouret G; Department of Pediatric Pulmonology and Allergology, Children's Hospital, Toulouse, France.
  • Coutier L; Department of Pediatric Pulmonology and Allergology, Reference Center for Cystic Fibrosis, Hôpital Mère Enfant, Bron, France.
  • Vuillerot C; U1028, CNRL, Lyon 1 University, Lyon, France.
  • Bieleu BM; Service de Rééducation Pédiatrique Infantile "L'Escale", Hôpital Mère Enfant, Hospices Civils de Lyon, Lyon, France.
  • Gomez Garcia de la Banda M; Neuromyogen Institute, CNRS UMR 5310-INSERM U1219, Lyon University, Lyon, France.
  • Corvol H; Department of Pediatric Neurology and ICU, AP-HP Université Paris Saclay, Hôpital Raymond Poincaré, Garches, France.
  • Servais L; Centre de Référence des Maladies Neuromusculaires Garches-Necker-Mondor-Hendaye (GNMH), Centre Nord- Est- Ile de France, Réseau national des maladies neuromusculaires, FILNEMUS, France.
  • Taytard J; European Reference Center Network (Euro-NMD ERN).
Pediatr Pulmonol ; 57(6): 1505-1512, 2022 06.
Article em En | MEDLINE | ID: mdl-35307979

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Ventilação não Invasiva Tipo de estudo: Guideline / Observational_studies / Risk_factors_studies Limite: Child / Female / Humans / Infant Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Ventilação não Invasiva Tipo de estudo: Guideline / Observational_studies / Risk_factors_studies Limite: Child / Female / Humans / Infant Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: França