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Efficacy and safety of lumasiran for infants and young children with primary hyperoxaluria type 1: 12-month analysis of the phase 3 ILLUMINATE-B trial.
Hayes, Wesley; Sas, David J; Magen, Daniella; Shasha-Lavsky, Hadas; Michael, Mini; Sellier-Leclerc, Anne-Laure; Hogan, Julien; Ngo, Taylor; Sweetser, Marianne T; Gansner, John M; McGregor, Tracy L; Frishberg, Yaacov.
Afiliação
  • Hayes W; Department of Paediatric Nephrology, Great Ormond Street Hospital, London, UK. Wesley.Hayes@gosh.nhs.uk.
  • Sas DJ; Division of Pediatric Nephrology and Hypertension, Mayo Clinic, Rochester, MN, USA.
  • Magen D; Pediatric Nephrology Institute, Rambam Health Care Campus, Haifa, Israel.
  • Shasha-Lavsky H; Paediatric Nephrology Unit, Galilee Medical Center, Nahariya, Israel.
  • Michael M; Division of Nephrology, Department of Pediatrics, Texas Children's Hospital, Baylor College of Medicine, Houston, TX, USA.
  • Sellier-Leclerc AL; Hôpital Femme Mère Enfant and Centre d'Investigation Clinique Inserm, Hospices Civils de Lyon, ERKnet, Bron, France.
  • Hogan J; Pediatric Nephrology Department, Hopital Robert-Debré, APHP, Paris, France.
  • Ngo T; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Sweetser MT; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Gansner JM; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • McGregor TL; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Frishberg Y; Division of Pediatric Nephrology, Shaare Zedek Medical Center and Faculty of Medicine, Hebrew University of Jerusalem, Jerusalem, Israel.
Pediatr Nephrol ; 38(4): 1075-1086, 2023 04.
Article em En | MEDLINE | ID: mdl-35913563

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hiperoxalúria Primária / Cálculos Renais Limite: Child / Child, preschool / Humans / Infant Idioma: En Revista: Pediatr Nephrol Assunto da revista: NEFROLOGIA / PEDIATRIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hiperoxalúria Primária / Cálculos Renais Limite: Child / Child, preschool / Humans / Infant Idioma: En Revista: Pediatr Nephrol Assunto da revista: NEFROLOGIA / PEDIATRIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Reino Unido