Impact of the Timing of Enzyme Replacement Therapy Initiation and Cognitive Impairment Status on Outcomes for Patients with Mucopolysaccharidosis II (MPS II) in the United States: A Retrospective Chart Review.
J Health Econ Outcomes Res
; 9(2): 67-76, 2022.
Article
em En
| MEDLINE
| ID: mdl-36168594
Texto completo:
1
Coleções:
01-internacional
Base de dados:
MEDLINE
Tipo de estudo:
Guideline
Idioma:
En
Revista:
J Health Econ Outcomes Res
Ano de publicação:
2022
Tipo de documento:
Article