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Early changes in bleeding perception and quality of life in children and adolescents receiving emicizumab prophylaxis for severe haemophilia A without inhibitor.
Marro, Marion; Petit, Audrey Françoise; Falaise, Céline; Roche, Martine; Gensollen, Sophie; Hezard, Nathalie; Boucekine, Mohamed; Auquier, Pascal; Chambost, Hervé; Saultier, Paul.
Afiliação
  • Marro M; Department of Pediatric Hematology, Immunology, and Oncology, APHM, La Timone Children's Hospital, Marseille, France.
  • Petit AF; Department of Pediatric Hematology, Immunology, and Oncology, APHM, La Timone Children's Hospital, Marseille, France.
  • Falaise C; Department of Pediatric Hematology, Immunology, and Oncology, APHM, La Timone Children's Hospital, Marseille, France.
  • Roche M; Department of Pediatric Hematology, Immunology, and Oncology, APHM, La Timone Children's Hospital, Marseille, France.
  • Gensollen S; Department of Pharmacy, APHM, La Conception Hospital, Marseille, France.
  • Hezard N; Laboratory of Hematology, APHM, La Timone Hospital, Marseille, France.
  • Boucekine M; CERESS, Aix Marseille Univ, Marseille, France.
  • Auquier P; CERESS, Aix Marseille Univ, Marseille, France.
  • Chambost H; Department of Pediatric Hematology, Immunology, and Oncology, APHM, La Timone Children's Hospital, Marseille, France.
  • Saultier P; INSERM, INRAe, C2VN, Aix Marseille Univ, Marseille, France.
Haemophilia ; 29(1): 397-400, 2023 Jan.
Article em En | MEDLINE | ID: mdl-36524683

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Anticorpos Biespecíficos / Hemofilia A Limite: Adolescent / Child / Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: França

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Anticorpos Biespecíficos / Hemofilia A Limite: Adolescent / Child / Humans Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: França