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Evinacumab in severe hypertriglyceridemia with or without lipoprotein lipase pathway mutations: a phase 2 randomized trial.
Rosenson, Robert S; Gaudet, Daniel; Ballantyne, Christie M; Baum, Seth J; Bergeron, Jean; Kershaw, Erin E; Moriarty, Patrick M; Rubba, Paolo; Whitcomb, David C; Banerjee, Poulabi; Gewitz, Andrew; Gonzaga-Jauregui, Claudia; McGinniss, Jennifer; Ponda, Manish P; Pordy, Robert; Zhao, Jian; Rader, Daniel J.
Afiliação
  • Rosenson RS; Metabolism and Lipids Unit, Mount Sinai Heart, Icahn School of Medicine at Mount Sinai, New York, NY, USA. robert.rosenson@mssm.edu.
  • Gaudet D; Clinical Lipidology and Rare Lipid Disorders Unit, Department of Medicine, Université de Montréal Community Gene Medicine Center, and ECOGENE-21 Clinical and Translational Research Center, Chicoutimi, Quebec, Canada.
  • Ballantyne CM; Department of Medicine, Baylor College of Medicine, Houston, TX, USA.
  • Baum SJ; Excel Medical Clinical Trials and Department of Integrated Medical Sciences, Charles E Schmidt College of Medicine, Florida Atlantic University, Boca Raton, FL, USA.
  • Bergeron J; Departments of Laboratory Medicine and of Medicine, Centre Hospitalier Universitaire de Québec-Université Laval, Québec, Québec, Canada.
  • Kershaw EE; Division of Endocrinology, Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
  • Moriarty PM; Division of Clinical Pharmacology, University of Kansas Medical Center, Kansas City, KS, USA.
  • Rubba P; Department of Clinical Medicine and Surgery, Federico II University of Naples, Naples, Italy.
  • Whitcomb DC; Division of Gastroenterology, Hepatology and Nutrition, University of Pittsburgh, Pittsburgh, PA, USA.
  • Banerjee P; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Gewitz A; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Gonzaga-Jauregui C; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • McGinniss J; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Ponda MP; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Pordy R; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Zhao J; Regeneron Pharmaceuticals, Tarrytown, NY, USA.
  • Rader DJ; Department of Genetics and Department of Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.
Nat Med ; 29(3): 729-737, 2023 03.
Article em En | MEDLINE | ID: mdl-36879129

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Pancreatite / Hipertrigliceridemia / Hiperlipoproteinemia Tipo I Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Female / Humans / Male Idioma: En Revista: Nat Med Assunto da revista: BIOLOGIA MOLECULAR / MEDICINA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Pancreatite / Hipertrigliceridemia / Hiperlipoproteinemia Tipo I Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Female / Humans / Male Idioma: En Revista: Nat Med Assunto da revista: BIOLOGIA MOLECULAR / MEDICINA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos