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Real-Life Outcome After Gene Replacement Therapy for Spinal Muscular Atrophy: A Multicenter Experience.
Tokatly Latzer, Itay; Sagi, Liora; Lavi, Revital; Aharoni, Sharon; Bistritzer, Jacob; Noyman, Iris; Ginsburg, Mira; Lev-Or, Angela; Katzenellenbogen, Sharona; Nevo, Yoram; Fattal-Valevski, Aviva.
Afiliação
  • Tokatly Latzer I; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel. Electronic address: itaylatzer@gmail.com.
  • Sagi L; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.
  • Lavi R; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.
  • Aharoni S; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel; Institute of Pediatric Neurology, Schneider Children's Medical Center of Israel, Petach Tikva, Israel.
  • Bistritzer J; Pediatric Neurology Unit, Soroka University Medical Center, Affiliated to the Ben-Gurion Faculty of Medicine, Beer-Sheva, Israel.
  • Noyman I; Pediatric Neurology Unit, Soroka University Medical Center, Affiliated to the Ben-Gurion Faculty of Medicine, Beer-Sheva, Israel.
  • Ginsburg M; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel; Pediatric Neurology Unit, Edith Wolfson Medical Center, Holon, Israel.
  • Lev-Or A; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel.
  • Katzenellenbogen S; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel.
  • Nevo Y; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel; Institute of Pediatric Neurology, Schneider Children's Medical Center of Israel, Petach Tikva, Israel.
  • Fattal-Valevski A; Pediatric Neurology Institute, The Dana-Dwek Children's Hospital, Tel Aviv Medical Center, Tel Aviv, Israel; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel; Incumbent, The Adler Chair in Pediatric Cardiology, Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.
Pediatr Neurol ; 144: 60-68, 2023 07.
Article em En | MEDLINE | ID: mdl-37149951

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância Tipo de estudo: Clinical_trials Limite: Child / Child, preschool / Humans / Infant / Newborn Idioma: En Revista: Pediatr Neurol Assunto da revista: NEUROLOGIA / PEDIATRIA Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância Tipo de estudo: Clinical_trials Limite: Child / Child, preschool / Humans / Infant / Newborn Idioma: En Revista: Pediatr Neurol Assunto da revista: NEUROLOGIA / PEDIATRIA Ano de publicação: 2023 Tipo de documento: Article