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ABE8e Corrects Pax6-Aniridic Variant in Humanized Mouse ESCs and via LNPs in Ex Vivo Cortical Neurons.
Adair, Bethany A; Korecki, Andrea J; Djaksigulova, Diana; Wagner, Pamela K; Chiu, Nina Y; Lam, Siu Ling; Lengyell, Tess C; Leavitt, Blair R; Simpson, Elizabeth M.
Afiliação
  • Adair BA; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Korecki AJ; Department of Medical Genetics, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Djaksigulova D; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Wagner PK; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Chiu NY; Incisive Genetics Inc., Vancouver, BC, Canada.
  • Lam SL; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Lengyell TC; Department of Medical Genetics, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Leavitt BR; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
  • Simpson EM; Centre for Molecular Medicine and Therapeutics at British Columbia Children's Hospital, The University of British Columbia, 950 West 28th Avenue, Vancouver, BC, V5Z 4H4, Canada.
Ophthalmol Ther ; 12(4): 2049-2068, 2023 Aug.
Article em En | MEDLINE | ID: mdl-37210469

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Ophthalmol Ther Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Canadá

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Ophthalmol Ther Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Canadá