Expression of NMNAT1 in the photoreceptors is sufficient to prevent <i>NMNAT1</i>-associated retinal degeneration.

Brown, Emily E; Scandura, Michael J; Pierce, Eric A

Expression of NMNAT1 in the photoreceptors is sufficient to prevent NMNAT1-associated retinal degeneration.

Brown, Emily E; Scandura, Michael J; Pierce, Eric A.

Afiliação

Brown EE; Ocular Genomics Institute, Department of Ophthalmology, Massachusetts Eye and Ear Harvard Medical School, Boston, MA 02114, USA.
Scandura MJ; Ocular Genomics Institute, Department of Ophthalmology, Massachusetts Eye and Ear Harvard Medical School, Boston, MA 02114, USA.
Pierce EA; Ocular Genomics Institute, Department of Ophthalmology, Massachusetts Eye and Ear Harvard Medical School, Boston, MA 02114, USA.

Mol Ther Methods Clin Dev ; 29: 319-328, 2023 Jun 08.

Article em En | MEDLINE | ID: mdl-37214313

Palavras-chave

AAV; IRD; LCA; NMNAT1; photoreceptors; promoters; retina; scAAV

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Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies / Risk_factors_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

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