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Simoctocog alfa (Nuwiq®) in previously untreated patients with severe haemophilia A-Final efficacy and safety results from the NuProtect study.
Mathias, Mary; Abraham, Aby; Belletrutti, Mark J; Carcao, Manuel; Carvalho, Manuela; Chambost, Hervé; Chan, Anthony K C; Dubey, Leonid; Ducore, Jonathan; Gattens, Michael; Gresele, Paolo; Gruel, Yves; Guillet, Benoit; Jiménez-Yuste, Victor; Kitanovski, Lidija; Klukowska, Anna; Lohade, Sunil; Mancuso, Maria Elisa; Oldenburg, Johannes; Pollio, Berardino; Sigaud, Marianne; Vilchevska, Kateryna; Wu, John K M; Jansen, Martina; Belyanskaya, Larisa; Walter, Olaf; Knaub, Sigurd; Neufeld, Ellis J.
Afiliação
  • Mathias M; Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Trust Haemophilia Centre, NIHR GOSH BRC, London, UK.
  • Abraham A; Department of Hematology, Christian Medical College, Vellore, India.
  • Belletrutti MJ; Department of Pediatrics, Division of Hematology/Oncology/BMT, University of British Columbia and British Columbia Children's Hospital, Vancouver, Canada.
  • Carcao M; Department of Paediatrics, Division of Haematology/Oncology and Child Health Evaluative Sciences, Research Institute Hospital for Sick Children, Toronto, Canada.
  • Carvalho M; Congenital Coagulopathies Reference Centre, São João University Hospital Centre, Porto, Portugal.
  • Chambost H; AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone, Aix Marseille Univ INSERM, INRA, C2VN, Marseille, France.
  • Chan AKC; Department of Pediatrics, McMaster Centre of Transfusion Research, McMaster University, Hamilton, Canada.
  • Dubey L; Department of Paediatrics, Western Ukrainian Specialized Children's Medical Centre, Lviv, Ukraine.
  • Ducore J; Department of Pediatrics, University of California Davis Medical Center, Sacramento, California, USA.
  • Gattens M; Department of Paediatric Haematology and Oncology, Addenbrooke's Hospital, Cambridge University Hospital NHS Foundation Trust, Cambridge, UK.
  • Gresele P; Department of Medicine and Surgery, University of Perugia, Perugia, Italy.
  • Gruel Y; Centre Régional de Traitement de l'Hémophilie, Hôpital Trousseau, Tours, France.
  • Guillet B; Haemophilia Treatment Centre, Univ Rennes, CHU Rennes, INSERM, EHESP, Irset (Institut de Recherche en Santé, Environnement et Travail) - UMR_S 1085, Rennes, France.
  • Jiménez-Yuste V; Servicio de Hematología, Hospital Univeristario La Paz, Autónoma, University of Madrid, Madrid, Spain.
  • Kitanovski L; Department of Haematooncology, Division of Paediatrics, University Medical Center Ljubljana, Ljubljana, Slovenia.
  • Klukowska A; Haemostasis Group of the Polish Society of Haematology and Transfusiology, Warsaw, Poland.
  • Lohade S; Department of Hematology, Sahyadri Speciality Hospital, Pune, India.
  • Mancuso ME; Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital, Milan, Italy.
  • Oldenburg J; Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn, Bonn, Germany.
  • Pollio B; Regional Reference Centre for Inherited Bleeding and Thrombotic Disorders, Regina Margherita Children Hospital, Turin, Italy.
  • Sigaud M; Centre Régional de Traitement de I'Hémophilie, University Hospital of Nantes, Nantes, France.
  • Vilchevska K; Department of Hematology, OHMATDYT - National Specialized Children's Hospital, Kiev, Ukraine.
  • Wu JKM; Department of Pediatrics, Division of Hematology/Oncology/BMT, University of British Columbia and British Columbia Children's Hospital, Vancouver, Canada.
  • Jansen M; Octapharma Pharmazeutika Produktionsges m.b.H, Vienna, Austria.
  • Belyanskaya L; Octapharma AG, Lachen, Switzerland.
  • Walter O; Octapharma AG, Lachen, Switzerland.
  • Knaub S; Octapharma AG, Lachen, Switzerland.
  • Neufeld EJ; Department of Hematology, St. Jude Children's Research Hospital, Memphis, Tennessee, USA.
Eur J Haematol ; 111(4): 544-552, 2023 Oct.
Article em En | MEDLINE | ID: mdl-37439123

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemofilia A Limite: Humans Idioma: En Revista: Eur J Haematol Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hemofilia A Limite: Humans Idioma: En Revista: Eur J Haematol Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Reino Unido