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Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy.
Obici, Laura; Ajroud-Driss, Senda; Lin, Kon-Ping; Berk, John L; Gillmore, Julian D; Kale, Parag; Koike, Haruki; Danese, David; Aldinc, Emre; Chen, Chongshu; Vest, John; Adams, David.
Afiliação
  • Obici L; Amyloidosis Research and Treatment Centre, IRCCS Fondazione Policlinico San Matteo, Pavia, Italy. LObici@smatteo.pv.it.
  • Ajroud-Driss S; Department of Neurology, Northwestern University Feinberg School of Medicine, Chicago, IL, USA.
  • Lin KP; Department of Neurology, Taipei Veterans General Hospital, Taipei, Taiwan.
  • Berk JL; Boston Medical Center, Boston, MA, USA.
  • Gillmore JD; National Amyloidosis Centre, Royal Free Hospital, University College London, London, UK.
  • Kale P; Baylor University Medical Center, Dallas, TX, USA.
  • Koike H; Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Danese D; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Aldinc E; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Chen C; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Vest J; Alnylam Pharmaceuticals, Cambridge, MA, USA.
  • Adams D; Neurology Department, Université Paris-Saclay, U1195, INSERM, AP-HP, CHU Bicêtre, Le Kremlin Bicêtre, France.
Neurol Ther ; 12(5): 1759-1775, 2023 Oct.
Article em En | MEDLINE | ID: mdl-37523143

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Clinical_trials / Screening_studies Idioma: En Revista: Neurol Ther Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Clinical_trials / Screening_studies Idioma: En Revista: Neurol Ther Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Itália