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Impact of nusinersen on the health-related quality of life and caregiver burden of patients with spinal muscular atrophy with symptom onset after age 6 months.
Lee, Yun Jeong; Kim, Ae Ryoung; Lee, Jong-Mok; Shim, Young Kyu; Cho, Jae So; Ryu, Hye Won; Kwon, Soonhak; Chae, Jong-Hee.
Afiliação
  • Lee YJ; Department of Pediatrics, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Kim AR; Department of Rehabilitation Medicine, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Lee JM; Department of Neurology, Kyungpook National University Hospital and School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Shim YK; Department of Pediatrics, Korea University Ansan Hospital, Seoul, South Korea.
  • Cho JS; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
  • Ryu HW; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
  • Kwon S; Department of Pediatrics, Kyungpook National University Children's Hospital, School of Medicine, Kyungpook National University, Daegu, South Korea.
  • Chae JH; Department of Pediatrics, Pediatric Clinical Neuroscience Center, Seoul National University Children's Hospital, Seoul National University College of Medicine, Seoul, South Korea.
Muscle Nerve ; 68(4): 404-413, 2023 10.
Article em En | MEDLINE | ID: mdl-37602664

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Sobrecarga do Cuidador Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Child / Humans / Infant Idioma: En Revista: Muscle Nerve Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Coréia do Sul

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Sobrecarga do Cuidador Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Child / Humans / Infant Idioma: En Revista: Muscle Nerve Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Coréia do Sul