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Unexpected extra exon skipping in the DYSF gene during restoring the reading frame by CRISPR/Cas9.
Levchenko, Olga; Panchuk, Irina; Kochergin-Nikitsky, Konstantin; Petrova, Irina; Nagieva, Sabina; Pilkin, Maxim; Yakovlev, Ivan; Smirnikhina, Svetlana; Deev, Roman; Lavrov, Alexander.
Afiliação
  • Levchenko O; Research Centre for Medical Genetics, 115522, Moscow, Russia. Electronic address: olevchenko@med-gen.ru.
  • Panchuk I; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Kochergin-Nikitsky K; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Petrova I; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Nagieva S; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Pilkin M; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Yakovlev I; Artgene Biotech PJSC, 119222, Moscow, Russia.
  • Smirnikhina S; Research Centre for Medical Genetics, 115522, Moscow, Russia.
  • Deev R; North-Western State Medical University named after I.I. Mechnikov, 191015, St. Petersburg, Russia.
  • Lavrov A; Research Centre for Medical Genetics, 115522, Moscow, Russia.
Biosystems ; 235: 105072, 2024 Jan.
Article em En | MEDLINE | ID: mdl-37944631

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Sistemas CRISPR-Cas / RNA Guia de Sistemas CRISPR-Cas Limite: Humans Idioma: En Revista: Biosystems Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Sistemas CRISPR-Cas / RNA Guia de Sistemas CRISPR-Cas Limite: Humans Idioma: En Revista: Biosystems Ano de publicação: 2024 Tipo de documento: Article