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Protein Delivery of an Artificial Transcription Factor Restores Widespread Ube3a Expression in an Angelman Syndrome Mouse Brain.
Bailus, Barbara J; Pyles, Benjamin; McAlister, Michelle M; O'Geen, Henriette; Lockwood, Sarah H; Adams, Alexa N; Nguyen, Jennifer Trang T; Yu, Abigail; Berman, Robert F; Segal, David J.
Afiliación
  • Bailus BJ; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Pyles B; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • McAlister MM; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • O'Geen H; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Lockwood SH; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Adams AN; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Nguyen JT; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Yu A; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
  • Berman RF; Department of Neurological Surgery, University of California, Davis, California, USA.
  • Segal DJ; Genome Center, MIND Institute, and Department of Biochemistry and Molecular Medicine, University of California, Davis, California, USA.
Mol Ther ; 24(3): 548-55, 2016 Mar.
Article en En | MEDLINE | ID: mdl-26727042

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Factores de Transcripción / Encéfalo / Regulación de la Expresión Génica / Síndrome de Angelman / Ubiquitina-Proteína Ligasas Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2016 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Factores de Transcripción / Encéfalo / Regulación de la Expresión Génica / Síndrome de Angelman / Ubiquitina-Proteína Ligasas Tipo de estudio: Prognostic_studies Límite: Animals Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2016 Tipo del documento: Article País de afiliación: Estados Unidos