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Gene-Corrected Fibroblast Therapy for Recessive Dystrophic Epidermolysis Bullosa using a Self-Inactivating COL7A1 Retroviral Vector.
Jacków, Joanna; Titeux, Matthias; Portier, Soizic; Charbonnier, Soëli; Ganier, Clarisse; Gaucher, Sonia; Hovnanian, Alain.
Afiliación
  • Jacków J; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France.
  • Titeux M; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France.
  • Portier S; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France.
  • Charbonnier S; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France.
  • Ganier C; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France.
  • Gaucher S; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France; Department of General Surgery, Plastic Surgery, and Ambulatory Surgery, AP-HP, HUPC, Cochin Hospital, Paris, France.
  • Hovnanian A; Laboratory of Genetic Skin Diseases, Inserm UMR1163 and Imagine Institute of Genetic Diseases, Paris, France; University Paris Descartes-Sorbonne Paris Cite, Paris, France; Department of Genetics, Necker Hospital, Paris, France. Electronic address: alain.hovnanian@inserm.fr.
J Invest Dermatol ; 136(7): 1346-1354, 2016 07.
Article en En | MEDLINE | ID: mdl-26994967

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Terapia Genética / Epidermólisis Ampollosa Distrófica / Colágeno Tipo VII / Fibroblastos Límite: Animals / Humans Idioma: En Revista: J Invest Dermatol Año: 2016 Tipo del documento: Article País de afiliación: Francia

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Terapia Genética / Epidermólisis Ampollosa Distrófica / Colágeno Tipo VII / Fibroblastos Límite: Animals / Humans Idioma: En Revista: J Invest Dermatol Año: 2016 Tipo del documento: Article País de afiliación: Francia