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Patient-Centered Therapy Development for Myotonic Dystrophy: Report of the Myotonic Dystrophy Foundation-Sponsored Workshop.
Hesterlee, Sharon; Amur, Shashi; Bain, Lisa J; Carulli, John; Clarke, Sarah; Day, John W; Gagnon, Cynthia; Hagerman, Katharine; Heatwole, Chad; Johnson, Nicholas E; Moxley, Richard; Patel, Nikunj; Thornton, Charles; Kessel, Woodie; White, Molly.
Afiliación
  • Hesterlee S; 1 Myotonic Dystrophy Foundation, San Francisco, CA, USA.
  • Amur S; 2 Office of Translational Sciences, CDER, FDA, Silver Spring, MD, USA.
  • Bain LJ; 3 Science Writer, Elverson, PA, USA.
  • Carulli J; 4 Precision Medicine, Biogen, Cambridge, MA, USA.
  • Clarke S; 5 Patient and caregiver, NY, USA.
  • Day JW; 6 Department of Neurology, School of Medicine, Stanford University, Palo Alto, CA, USA.
  • Gagnon C; 7 School of Rehabilitation, Université de Sherbrooke, Quebec, Canada.
  • Hagerman K; 6 Department of Neurology, School of Medicine, Stanford University, Palo Alto, CA, USA.
  • Heatwole C; 8 Department of Neurology, School of Medicine and Dentistry, University of Rochester, Rochester, NY, USA.
  • Johnson NE; 9 Department of Neurology, School of Medicine, University of Utah, Salt Lake City, UT, USA.
  • Moxley R; 8 Department of Neurology, School of Medicine and Dentistry, University of Rochester, Rochester, NY, USA.
  • Patel N; 10 Office of New Drugs, CDER, FDA, Silver Spring, MD, USA.
  • Thornton C; 8 Department of Neurology, School of Medicine and Dentistry, University of Rochester, Rochester, NY, USA.
  • Kessel W; 1 Myotonic Dystrophy Foundation, San Francisco, CA, USA.
  • White M; 1 Myotonic Dystrophy Foundation, San Francisco, CA, USA.
Ther Innov Regul Sci ; 51(4): 516-522, 2017 Jul.
Article en En | MEDLINE | ID: mdl-30227044

Texto completo: 1 Banco de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Ther Innov Regul Sci Año: 2017 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Banco de datos: MEDLINE Tipo de estudio: Risk_factors_studies Idioma: En Revista: Ther Innov Regul Sci Año: 2017 Tipo del documento: Article País de afiliación: Estados Unidos