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Disease pharmacokinetic-pharmacodynamic modelling in acute intermittent porphyria to support the development of mRNA-based therapies.
Parra-Guillen, Zinnia P; Fontanellas, Antonio; Jiang, Lei; Jericó, Daniel; Martini, Paolo; Vera-Yunca, Diego; Hard, Marjie; Guey, Lin T; Troconiz, Iñaki F.
Afiliación
  • Parra-Guillen ZP; Department of Pharmaceutical Technology and Chemistry, School of Pharmacy and Nutrition, University of Navarra, Pamplona, Spain.
  • Fontanellas A; Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Jiang L; Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Jericó D; Hepatology Program, Centre for Applied Medical Research, University of Navarra, Pamplona, Spain.
  • Martini P; Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBEREHD), Instituto de Salud Carlos III, Madrid, Spain.
  • Vera-Yunca D; Moderna, Inc, Cambridge, Massachusetts.
  • Hard M; Hepatology Program, Centre for Applied Medical Research, University of Navarra, Pamplona, Spain.
  • Guey LT; Moderna, Inc, Cambridge, Massachusetts.
  • Troconiz IF; Department of Pharmaceutical Technology and Chemistry, School of Pharmacy and Nutrition, University of Navarra, Pamplona, Spain.
Br J Pharmacol ; 177(14): 3168-3182, 2020 07.
Article en En | MEDLINE | ID: mdl-32133631

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Porfiria Intermitente Aguda Límite: Animals Idioma: En Revista: Br J Pharmacol Año: 2020 Tipo del documento: Article País de afiliación: España

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Porfiria Intermitente Aguda Límite: Animals Idioma: En Revista: Br J Pharmacol Año: 2020 Tipo del documento: Article País de afiliación: España