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Single-Dose Pharmacokinetics and Pharmacodynamics of Transthyretin Targeting N-acetylgalactosamine-Small Interfering Ribonucleic Acid Conjugate, Vutrisiran, in Healthy Subjects.
Habtemariam, Bahru A; Karsten, Verena; Attarwala, Husain; Goel, Varun; Melch, Megan; Clausen, Valerie A; Garg, Pushkal; Vaishnaw, Akshay K; Sweetser, Marianne T; Robbie, Gabriel J; Vest, John.
Afiliación
  • Habtemariam BA; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Karsten V; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Attarwala H; Moderna Therapeutics, Cambridge, Massachusetts, USA.
  • Goel V; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Melch M; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Clausen VA; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Garg P; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Vaishnaw AK; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Sweetser MT; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Robbie GJ; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
  • Vest J; Alnylam Pharmaceuticals, Cambridge, Massachusetts, USA.
Clin Pharmacol Ther ; 109(2): 372-382, 2021 02.
Article en En | MEDLINE | ID: mdl-32599652

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Acetilgalactosamina / Prealbúmina / ARN / Neuropatías Amiloides Familiares Tipo de estudio: Clinical_trials Límite: Adult / Female / Humans / Male Idioma: En Revista: Clin Pharmacol Ther Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Acetilgalactosamina / Prealbúmina / ARN / Neuropatías Amiloides Familiares Tipo de estudio: Clinical_trials Límite: Adult / Female / Humans / Male Idioma: En Revista: Clin Pharmacol Ther Año: 2021 Tipo del documento: Article País de afiliación: Estados Unidos