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Ivacaftor in People with Cystic Fibrosis and a 3849+10kb C→T or D1152H Residual Function Mutation.
Kerem, Eitan; Cohen-Cymberknoh, Malena; Tsabari, Reuven; Wilschanski, Michael; Reiter, Joel; Shoseyov, David; Gileles-Hillel, Alex; Pugatsch, Thea; Davies, Jane C; Short, Christopher; Saunders, Clare; DeSouza, Cynthia; Sullivan, James C; Doyle, Jamie R; Chandarana, Keval; Kinnman, Nils.
Afiliación
  • Kerem E; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Cohen-Cymberknoh M; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Tsabari R; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Wilschanski M; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Reiter J; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Shoseyov D; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Gileles-Hillel A; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Pugatsch T; Department of Pediatrics and Cystic Fibrosis Center, Hadassah-Hebrew University Medical Center, Mount Scopus, Jerusalem, Israel.
  • Davies JC; European Cystic Fibrosis Society Lung Clearance Index Core Over Reading Centre, London, United Kingdom.
  • Short C; National Heart and Lung Institute, Imperial College London, London, United Kingdom.
  • Saunders C; Royal Brompton & Harefield National Health Service Foundation Trust, London, United Kingdom.
  • DeSouza C; European Cystic Fibrosis Society Lung Clearance Index Core Over Reading Centre, London, United Kingdom.
  • Sullivan JC; National Heart and Lung Institute, Imperial College London, London, United Kingdom.
  • Doyle JR; Royal Brompton & Harefield National Health Service Foundation Trust, London, United Kingdom.
  • Chandarana K; European Cystic Fibrosis Society Lung Clearance Index Core Over Reading Centre, London, United Kingdom.
  • Kinnman N; National Heart and Lung Institute, Imperial College London, London, United Kingdom.
Ann Am Thorac Soc ; 18(3): 433-441, 2021 03.
Article en En | MEDLINE | ID: mdl-33095038

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Fibrosis Quística Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Humans Idioma: En Revista: Ann Am Thorac Soc Año: 2021 Tipo del documento: Article País de afiliación: Israel

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Fibrosis Quística Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Humans Idioma: En Revista: Ann Am Thorac Soc Año: 2021 Tipo del documento: Article País de afiliación: Israel