Correction of RNA splicing defect in ß<sup>654</sup>-thalassemia mice using CRISPR/Cas9 gene-editing technology.

Correction of RNA splicing defect in ß⁶⁵⁴-thalassemia mice using CRISPR/Cas9 gene-editing technology.

Lu, Dan; Gong, Xiuli; Fang, Yudan; Guo, Xinbing; Chen, Yanwen; Yang, Fan; Zhao, Guijun; Ma, Qingwen; Zeng, Yitao; Zeng, Fanyi.

Afiliación

Lu D; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Gong X; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Fang Y; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Guo X; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Chen Y; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Yang F; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Zhao G; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Ma Q; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Zeng Y; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040.
Zeng F; Shanghai Institute of Medical Genetics, Shanghai Children's Hospital, Shanghai Jiao Tong University, Shanghai 200040, China; Department of Histo-Embryology, Genetics and Developmental Biology, Shanghai Jiao Tong University School of Medicine, Shanghai, 200025, China; Key Laboratory of Embryo Molecul

Haematologica ; 107(6): 1427-1437, 2022 Jun 01.

Article en En | MEDLINE | ID: mdl-34706494

Texto completo: 1 Banco de datos: MEDLINE Idioma: En Revista: Haematologica Año: 2022 Tipo del documento: Article

Texto completo: 1 Banco de datos: MEDLINE Idioma: En Revista: Haematologica Año: 2022 Tipo del documento: Article