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Effects of Elexacaftor/Tezacaftor/Ivacaftor Therapy on CFTR Function in Patients with Cystic Fibrosis and One or Two F508del Alleles.
Graeber, Simon Y; Vitzthum, Constanze; Pallenberg, Sophia T; Naehrlich, Lutz; Stahl, Mirjam; Rohrbach, Alexander; Drescher, Marika; Minso, Rebecca; Ringshausen, Felix C; Rueckes-Nilges, Claudia; Klajda, Jan; Berges, Julian; Yu, Yin; Scheuermann, Heike; Hirtz, Stephanie; Sommerburg, Olaf; Dittrich, Anna-Maria; Tümmler, Burkhard; Mall, Marcus A.
Afiliación
  • Graeber SY; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany.
  • Vitzthum C; Berlin Institute of Health at Charité-Universitätsmedizin Berlin, Berlin, Germany.
  • Pallenberg ST; German Center for Lung Research, associated partner site, Berlin, Germany.
  • Naehrlich L; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany.
  • Stahl M; German Center for Lung Research, associated partner site, Berlin, Germany.
  • Rohrbach A; Department of Pediatric Pneumology, Allergology and Neonatology.
  • Drescher M; Biomedical Research in Endstage and Obstructive Lung Disease Hannover, German Center for Lung Research, and.
  • Minso R; Department of Pediatrics, Justus-Liebig-University Giessen, Giessen, Germany.
  • Ringshausen FC; Universities of Giessen and Marburg Lung Center, German Center for Lung Research, Giessen, Germany; and.
  • Rueckes-Nilges C; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany.
  • Klajda J; Berlin Institute of Health at Charité-Universitätsmedizin Berlin, Berlin, Germany.
  • Berges J; German Center for Lung Research, associated partner site, Berlin, Germany.
  • Yu Y; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany.
  • Scheuermann H; German Center for Lung Research, associated partner site, Berlin, Germany.
  • Hirtz S; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine and Cystic Fibrosis Center, Charité-Universitätsmedizin Berlin, corporate member of Freie Universität Berlin and Humboldt-Universität zu Berlin, Berlin, Germany.
  • Sommerburg O; German Center for Lung Research, associated partner site, Berlin, Germany.
  • Dittrich AM; Department of Pediatric Pneumology, Allergology and Neonatology.
  • Tümmler B; Biomedical Research in Endstage and Obstructive Lung Disease Hannover, German Center for Lung Research, and.
  • Mall MA; Department of Respiratory Medicine, Hannover Medical School, Hannover, Germany.
Am J Respir Crit Care Med ; 205(5): 540-549, 2022 03 01.
Article en En | MEDLINE | ID: mdl-34936849

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Humans Idioma: En Revista: Am J Respir Crit Care Med Asunto de la revista: TERAPIA INTENSIVA Año: 2022 Tipo del documento: Article País de afiliación: Alemania

Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística Tipo de estudio: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Límite: Humans Idioma: En Revista: Am J Respir Crit Care Med Asunto de la revista: TERAPIA INTENSIVA Año: 2022 Tipo del documento: Article País de afiliación: Alemania