Is treatment with oral risdiplam effective and well-tolerated for infants with spinal muscular atrophy type 1?

Gaffar, Sheema; Cayabyab, Rowena; Ramanathan, Rangasamy

Gaffar, Sheema; Cayabyab, Rowena; Ramanathan, Rangasamy.

Afiliación

Gaffar S; Division of Neonatology, Department of Pediatrics, LAC+USC Medical Center, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA. gaffar@usc.edu.
Cayabyab R; Division of Neonatology, Department of Pediatrics, LAC+USC Medical Center, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
Ramanathan R; Division of Neonatology, Department of Pediatrics, LAC+USC Medical Center, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.

J Perinatol ; 42(5): 689-691, 2022 05.

Article en En | MEDLINE | ID: mdl-35095098

Asunto(s)

Atrofias Musculares Espinales de la Infancia; Compuestos Azo; Humanos; Lactante; Pirimidinas; Atrofias Musculares Espinales de la Infancia/tratamiento farmacológico

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Texto completo: 1 Banco de datos: MEDLINE Asunto principal: Atrofias Musculares Espinales de la Infancia Límite: Humans / Infant Idioma: En Revista: J Perinatol Asunto de la revista: PERINATOLOGIA Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

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