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Gene therapy targeting oligodendrocytes provides therapeutic benefit in a leukodystrophy model.
Georgiou, Elena; Sidiropoulou, Kyriaki; Richter, Jan; Papaneophytou, Christos; Sargiannidou, Irene; Kagiava, Alexia; von Jonquieres, Georg; Christodoulou, Christina; Klugmann, Matthias; Kleopa, Kleopas A.
Afiliación
  • Georgiou E; Neuroscience Laboratory, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Sidiropoulou K; Department of Zoology, University of Crete, Heraklion, Greece.
  • Richter J; Department of Molecular Virology, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Papaneophytou C; Neuroscience Laboratory, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Sargiannidou I; Neuroscience Laboratory, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Kagiava A; Neuroscience Laboratory, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • von Jonquieres G; Translational Neuroscience Facility and Department of Physiology, School of Medical Sciences, University of New South Wales, Sydney, Australia.
  • Christodoulou C; Department of Molecular Virology, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
  • Klugmann M; Translational Neuroscience Facility and Department of Physiology, School of Medical Sciences, University of New South Wales, Sydney, Australia.
  • Kleopa KA; Neuroscience Laboratory, The Cyprus Institute of Neurology and Genetics and Cyprus School of Molecular Medicine, Nicosia, Cyprus.
Brain ; 140(3): 599-616, 2017 03 01.
Article en En | MEDLINE | ID: mdl-28100454

Texto completo: 1 Colección: 01-internacional Asunto principal: Terapia Genética / Oligodendroglía / Regulación de la Expresión Génica / Modelos Animales de Enfermedad / Leucoencefalopatías Tipo de estudio: Etiology_studies Límite: Animals / Humans Idioma: En Revista: Brain Año: 2017 Tipo del documento: Article País de afiliación: Chipre

Texto completo: 1 Colección: 01-internacional Asunto principal: Terapia Genética / Oligodendroglía / Regulación de la Expresión Génica / Modelos Animales de Enfermedad / Leucoencefalopatías Tipo de estudio: Etiology_studies Límite: Animals / Humans Idioma: En Revista: Brain Año: 2017 Tipo del documento: Article País de afiliación: Chipre