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Caution advised in the use of CFTR modulator treatment for individuals harboring specific CFTR variants.
Raraigh, Karen S; Lewis, Michelle H; Collaco, Joseph M; Corey, Mary; Penland, Christopher M; Stephenson, Anne L; Rommens, Johanna M; Castellani, Carlo; Cutting, Garry R.
Afiliación
  • Raraigh KS; McKusick-Nathans Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21287, United States.
  • Lewis MH; Berman Institute of Bioethics, Johns Hopkins University, Baltimore, MD 21287, United States.
  • Collaco JM; Eudowood Division of Pediatric Respiratory Sciences, Johns Hopkins University School of Medicine, Baltimore, MD 21287, United States.
  • Corey M; Child Health Evaluative Sciences, The Hospital for Sick Children, Toronto, Ontario, Canada.
  • Penland CM; Cystic Fibrosis Foundation, Bethesda, MD 20814, United States.
  • Stephenson AL; Department of Respirology, Adult Cystic Fibrosis Program, St. Michael's Hospital, Toronto, Ontario, Canada.
  • Rommens JM; Program in Genetics and Genome Biology, The Hospital for Sick Children, Toronto, Ontario, Canada.
  • Castellani C; IRCCS Istituto Giannina Gaslini, Cystic Fibrosis Center, Genoa, Italy.
  • Cutting GR; McKusick-Nathans Department of Genetic Medicine, Johns Hopkins University School of Medicine, Baltimore, MD 21287, United States. Electronic address: gcutting@jhmi.edu.
J Cyst Fibros ; 21(5): 856-860, 2022 09.
Article en En | MEDLINE | ID: mdl-35527187

Texto completo: 1 Colección: 01-internacional Asunto principal: Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística Límite: Humans Idioma: En Revista: J Cyst Fibros Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Asunto principal: Regulador de Conductancia de Transmembrana de Fibrosis Quística / Fibrosis Quística Límite: Humans Idioma: En Revista: J Cyst Fibros Año: 2022 Tipo del documento: Article País de afiliación: Estados Unidos