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Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results.
Lam, Byron L; Davis, Janet L; Gregori, Ninel Z; MacLaren, Robert E; Girach, Aniz; Verriotto, Jennifer D; Rodriguez, Belen; Rosa, Potyra R; Zhang, Xiaojun; Feuer, William J.
Afiliação
  • Lam BL; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA. Electronic address: blam@med.miami.edu.
  • Davis JL; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • Gregori NZ; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • MacLaren RE; Nuffield Laboratory of Ophthalmology University of Oxford, and Oxford NIHR Biomedical Research Centre, Oxford, United Kingdom.
  • Girach A; Nightstar Therapeutics, London, United Kingdom.
  • Verriotto JD; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • Rodriguez B; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • Rosa PR; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • Zhang X; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
  • Feuer WJ; Bascom Palmer Eye Institute, University of Miami Miller School of Medicine, Miami, Florida, USA.
Am J Ophthalmol ; 197: 65-73, 2019 01.
Article em En | MEDLINE | ID: mdl-30240725

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Terapia Genética / Coroideremia Limite: Adult / Aged / Humans / Male / Middle aged Idioma: En Revista: Am J Ophthalmol Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Terapia Genética / Coroideremia Limite: Adult / Aged / Humans / Male / Middle aged Idioma: En Revista: Am J Ophthalmol Ano de publicação: 2019 Tipo de documento: Article