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Therapeutic Options for Mucopolysaccharidoses: Current and Emerging Treatments.
Sawamoto, Kazuki; Stapleton, Molly; Alméciga-Díaz, Carlos J; Espejo-Mojica, Angela J; Losada, Juan Camilo; Suarez, Diego A; Tomatsu, Shunji.
Afiliação
  • Sawamoto K; Nemours Biomedical Research, Nemours/Alfred I. duPont Hospital for Children, 1600 Rockland Rd, Wilmington, DE, 19899-0269, USA.
  • Stapleton M; Nemours Biomedical Research, Nemours/Alfred I. duPont Hospital for Children, 1600 Rockland Rd, Wilmington, DE, 19899-0269, USA.
  • Alméciga-Díaz CJ; Department of Biological Sciences, University of Delaware, Newark, DE, USA.
  • Espejo-Mojica AJ; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Bogotá, DC, Colombia.
  • Losada JC; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Bogotá, DC, Colombia.
  • Suarez DA; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Bogotá, DC, Colombia.
  • Tomatsu S; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Bogotá, DC, Colombia.
Drugs ; 79(10): 1103-1134, 2019 Jul.
Article em En | MEDLINE | ID: mdl-31209777

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Mucopolissacaridoses Tipo de estudo: Screening_studies Limite: Adolescent / Adult / Child / Child, preschool / Humans / Infant / Newborn Idioma: En Revista: Drugs Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Mucopolissacaridoses Tipo de estudo: Screening_studies Limite: Adolescent / Adult / Child / Child, preschool / Humans / Infant / Newborn Idioma: En Revista: Drugs Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Estados Unidos