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Cystinosis: Therapy adherence and metabolic monitoring in patients treated with immediate-release cysteamine.
Linden, Simone; Klank, Sabrina; Harms, Erik; Grüneberg, Marianne; Park, Julien H; Marquardt, Thorsten.
Afiliação
  • Linden S; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
  • Klank S; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
  • Harms E; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
  • Grüneberg M; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
  • Park JH; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
  • Marquardt T; Department of General Pediatrics, Metabolic Diseases, University Children's Hospital, Albert-Schweitzer-Campus 1, Münster, NRW DE 48149, Germany.
Mol Genet Metab Rep ; 24: 100620, 2020 Sep.
Article em En | MEDLINE | ID: mdl-32685378

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Idioma: En Revista: Mol Genet Metab Rep Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Idioma: En Revista: Mol Genet Metab Rep Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Alemanha