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L-leucine improves anemia and growth in patients with transfusion-dependent Diamond-Blackfan anemia: Results from a multicenter pilot phase I/II study from the Diamond-Blackfan Anemia Registry.
Vlachos, Adrianna; Atsidaftos, Evangelia; Lababidi, Mohammad Lutfi; Muir, Ellen; Rogers, Zora R; Alhushki, Waseem; Bernstein, Jonathan; Glader, Bertil; Gruner, Barbara; Hartung, Helge; Knoll, Christine; Loew, Thomas; Nalepa, Grzegorz; Narla, Anupama; Panigrahi, Arun R; Sieff, Colin A; Walkovich, Kelly; Farrar, Jason E; Lipton, Jeffrey M.
Afiliação
  • Vlachos A; Feinstein Institutes for Medical Research, Northwell Health, Manhasset, New York.
  • Atsidaftos E; Division of Hematology/Oncology and Cellular Therapy, Cohen Children's Medical Center, Northwell Health, New Hyde Park, New York.
  • Lababidi ML; Feinstein Institutes for Medical Research, Northwell Health, Manhasset, New York.
  • Muir E; Division of Hematology/Oncology and Cellular Therapy, Cohen Children's Medical Center, Northwell Health, New Hyde Park, New York.
  • Rogers ZR; Feinstein Institutes for Medical Research, Northwell Health, Manhasset, New York.
  • Alhushki W; Feinstein Institutes for Medical Research, Northwell Health, Manhasset, New York.
  • Bernstein J; Division of Hematology/Oncology and Cellular Therapy, Cohen Children's Medical Center, Northwell Health, New Hyde Park, New York.
  • Glader B; University of Texas Southwestern Medical Center at Dallas, Dallas, Texas.
  • Gruner B; Pediatric Hematology Oncology, Cure4 The Kids Foundation, Las Vegas, Nevada.
  • Hartung H; Pediatric Hematology Oncology, Cure 4 The Kids Foundation, Las Vegas, Nevada; presently at Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania.
  • Knoll C; Division of Pediatric Hematology/Oncology, Stanford University School of Medicine, Stanford, California.
  • Loew T; Division of Pediatric Hematology/Oncology, University of Missouri, Columbia, Missouri.
  • Nalepa G; Division of Hematology, The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.
  • Narla A; The Center for Cancer and Blood Disorders, Phoenix Children's Hospital, Phoenix, Arizona.
  • Panigrahi AR; Division of Pediatric Hematology/Oncology, University of Missouri, Columbia, Missouri; presently at University of Kansas Medical Center, Kansas City, Kansas.
  • Sieff CA; Department of Pediatric Hematology-Oncology, Indiana University School of Medicine, Indianapolis, Indiana.
  • Walkovich K; Division of Pediatric Hematology/Oncology, Stanford University School of Medicine, Stanford, California.
  • Farrar JE; University of Louisville, Louisville, Kentucky; presently at University of California Davis, Sacramento, California.
  • Lipton JM; Harvard Medical School, Dana-Farber and Boston Children's, Cancer and Blood Disorders Center, Boston, Massachusetts.
Pediatr Blood Cancer ; 67(12): e28748, 2020 12.
Article em En | MEDLINE | ID: mdl-33025707

Texto completo: 1 Coleções: 01-internacional Temas: Geral / Prevencao_e_fatores_de_risco / Hereditariedade / Tratamento Base de dados: MEDLINE Assunto principal: Transfusão de Sangue / Anemia de Diamond-Blackfan / Leucina Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Revista: Pediatr Blood Cancer Assunto da revista: HEMATOLOGIA / NEOPLASIAS / PEDIATRIA Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Temas: Geral / Prevencao_e_fatores_de_risco / Hereditariedade / Tratamento Base de dados: MEDLINE Assunto principal: Transfusão de Sangue / Anemia de Diamond-Blackfan / Leucina Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male / Middle aged Idioma: En Revista: Pediatr Blood Cancer Assunto da revista: HEMATOLOGIA / NEOPLASIAS / PEDIATRIA Ano de publicação: 2020 Tipo de documento: Article