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Gene Therapy in a Mouse Model of Niemann-Pick Disease Type C1.
Kurokawa, Yoshie; Osaka, Hitoshi; Kouga, Takeshi; Jimbo, Eriko; Muramatsu, Kazuhiro; Nakamura, Sachie; Takayanagi, Yuki; Onaka, Tatsushi; Muramatsu, Shin-Ichi; Yamagata, Takanori.
Afiliação
  • Kurokawa Y; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Osaka H; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Kouga T; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Jimbo E; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Muramatsu K; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Nakamura S; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Takayanagi Y; Division of Brain and Neurophysiology, Department of Physiology, Jichi Medical University, Tochigi, Japan.
  • Onaka T; Division of Brain and Neurophysiology, Department of Physiology, Jichi Medical University, Tochigi, Japan.
  • Muramatsu SI; Division of Neurological Gene Therapy, Center for Open Innovation, Jichi Medical University, Tochigi, Japan.
  • Yamagata T; Center for Gene and Cell Therapy, The Institute of Medical Science, The University of Tokyo, Tokyo, Japan.
Hum Gene Ther ; 32(11-12): 589-598, 2021 06.
Article em En | MEDLINE | ID: mdl-33256498

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo C Limite: Animals / Humans Idioma: En Revista: Hum Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Doença de Niemann-Pick Tipo C Limite: Animals / Humans Idioma: En Revista: Hum Gene Ther Assunto da revista: GENETICA MEDICA / TERAPEUTICA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Japão