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VOCAL: An observational study of ivacaftor for people with cystic fibrosis and selected non-G551D-CFTR gating mutations.
Simmonds, Nicholas J; van der Ent, C Kors; Colombo, Carla; Kinnman, Nils; DeSouza, Cynthia; Thorat, Teja; Chew, Marci L; Chandarana, Keval; Castellani, Carlo.
Afiliação
  • Simmonds NJ; Adult Cystic Fibrosis Centre, Royal Brompton Hospital, London, UK, and National Heart and Lung Institute, Imperial College London, London, UK. Electronic address: n.simmonds@rbht.nhs.uk.
  • van der Ent CK; Department of Pediatric Respiratory Diseases, University Medical Center Utrecht, Utrecht, the Netherlands.
  • Colombo C; Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, University of Milan, Milan, Italy.
  • Kinnman N; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • DeSouza C; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Thorat T; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Chew ML; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Chandarana K; Vertex Pharmaceuticals Incorporated, Boston, MA, USA.
  • Castellani C; Cystic Fibrosis Centre, IRCCS Istituto Giannina Gaslini, Genoa, Italy.
J Cyst Fibros ; 22(1): 124-131, 2023 01.
Article em En | MEDLINE | ID: mdl-35613999

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Fibrose Cística Tipo de estudo: Observational_studies / Prognostic_studies Limite: Humans Idioma: En Revista: J Cyst Fibros Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Temas: Geral Base de dados: MEDLINE Assunto principal: Fibrose Cística Tipo de estudo: Observational_studies / Prognostic_studies Limite: Humans Idioma: En Revista: J Cyst Fibros Ano de publicação: 2023 Tipo de documento: Article