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1.
Duchenne muscular dystrophy cell culture models created by CRISPR/Cas9 gene editing and their application in drug screening.
Sci Rep
; 11(1): 18188, 2021 09 14.
Article
in English
| MEDLINE | ID: mdl-34521928
2.
A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures.
PLoS One
; 13(10): e0204485, 2018.
Article
in English
| MEDLINE | ID: mdl-30278058
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