Detalhe da pesquisa
1.
An evolved AAV variant enables efficient genetic engineering of murine T cells.
Cell
; 186(2): 446-460.e19, 2023 01 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-36638795
2.
The NIH Somatic Cell Genome Editing program.
Nature
; 592(7853): 195-204, 2021 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-33828315
3.
Engineered IgM and IgG cleaving enzymes for mitigating antibody neutralization and complement activation in AAV gene transfer.
Mol Ther
; 2024 May 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-38715362
4.
Gene Delivery From Granular Scaffolds for Tunable Biologics Manufacturing.
Small
; : e2309911, 2024 Mar 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-38462954
5.
Transgenic mice for in vivo epigenome editing with CRISPR-based systems.
Nat Methods
; 18(8): 965-974, 2021 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-34341582
6.
Interplay between Furin and Sialoglycans in Modulating Adeno-Associated Viral Cell Entry.
J Virol
; 97(5): e0009323, 2023 05 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-37097176
7.
Redirecting AAV vectors to extrahepatic tissues.
Mol Ther
; 31(12): 3371-3375, 2023 Dec 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-37805712
8.
Efficient Adeno-associated Virus-mediated Transgenesis in Alveolar Stem Cells and Associated Niches.
Am J Respir Cell Mol Biol
; 69(3): 255-265, 2023 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-37315312
9.
Epigenetic Silencing of Recombinant Adeno-associated Virus Genomes by NP220 and the HUSH Complex.
J Virol
; 96(4): e0203921, 2022 02 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-34878926
10.
Structurally Mapping Antigenic Epitopes of Adeno-associated Virus 9: Development of Antibody Escape Variants.
J Virol
; 96(3): e0125121, 2022 02 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-34757842
11.
Receptor Switching in Newly Evolved Adeno-associated Viruses.
J Virol
; 95(19): e0058721, 2021 09 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-34232726
12.
Full-length dystrophin restoration via targeted exon integration by AAV-CRISPR in a humanized mouse model of Duchenne muscular dystrophy.
Mol Ther
; 29(11): 3243-3257, 2021 11 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-34509668
13.
Coevolution of Adeno-associated Virus Capsid Antigenicity and Tropism through a Structure-Guided Approach.
J Virol
; 94(19)2020 09 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-32669336
14.
The Golgi Calcium ATPase Pump Plays an Essential Role in Adeno-associated Virus Trafficking and Transduction.
J Virol
; 94(21)2020 10 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-32817219
15.
Ring finger protein 121 is a potent regulator of adeno-associated viral genome transcription.
PLoS Pathog
; 15(8): e1007988, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31386698
16.
Characterization of liver GSD IX γ2 pathophysiology in a novel Phkg2-/- mouse model.
Mol Genet Metab
; 133(3): 269-276, 2021 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-34083142
17.
Optimizing delivery for efficient cardiac reprogramming.
Biochem Biophys Res Commun
; 533(1): 9-16, 2020 11 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-32917363
18.
Modulation of Sialic Acid Dependence Influences the Central Nervous System Transduction Profile of Adeno-associated Viruses.
J Virol
; 93(11)2019 06 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30894463
19.
A CRISPR Screen Identifies the Cell Polarity Determinant Crumbs 3 as an Adeno-associated Virus Restriction Factor in Hepatocytes.
J Virol
; 93(21)2019 11 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31391273
20.
Vaccine-Mediated Inhibition of the Transporter Associated with Antigen Processing Is Insufficient To Induce Major Histocompatibility Complex E-Restricted CD8+ T Cells in Nonhuman Primates.
J Virol
; 93(19)2019 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31315990