Detalhe da pesquisa
1.
Strategic infection prevention after genetically modified hematopoietic stem cell therapies: recommendations from the International Society for Cell & Gene Therapy Stem Cell Engineering Committee.
Cytotherapy
; 2024 Feb 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-38483362
2.
Editing human hematopoietic stem cells: advances and challenges.
Cytotherapy
; 25(3): 261-269, 2023 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-36123234
3.
Early immune reconstitution as predictor for outcomes after allogeneic hematopoietic cell transplant; a tri-institutional analysis.
Cytotherapy
; 25(9): 977-985, 2023 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-37330731
4.
International Society for Cell & Gene Therapy Stem Cell Engineering Committee: Cellular therapies for the treatment of graft-versus-host-disease after hematopoietic stem cell transplant.
Cytotherapy
; 25(6): 578-589, 2023 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-36941149
5.
Novel Score to Predict Immunoglobulin Resistance in Kawasaki Disease.
Pediatr Cardiol
; 44(7): 1546-1551, 2023 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-37173579
6.
Reduced-intensity conditioning-based hematopoietic cell transplantation for dyskeratosis congenita: Single-center experience and literature review.
Pediatr Blood Cancer
; 68(10): e29177, 2021 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-34086408
7.
Correction: Novel Score to Predict Immunoglobulin Resistance in Kawasaki Disease.
Pediatr Cardiol
; 44(7): 1638-1639, 2023 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-37530798
8.
The successful use of eculizumab for treatment of thrombotic microangiopathy in pediatric acute SARSCoV2 infection and multisystem inflammatory syndrome in children.
Haematologica
; 107(10): 2517-2522, 2022 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-35615927
9.
Dysphagia and Epigastric Pain in an Adolescent Boy.
Pediatr Rev
; 42(4): 209-211, 2021 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-33795468
10.
Use of caplacizumab in a child with refractory thrombotic thrombocytopenic purpura.
Pediatr Blood Cancer
; 66(7): e27737, 2019 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30924605
11.
Visual Diagnosis: Teenager with Fever, Petechiae, Confusion, and Weakness.
Pediatr Rev
; 40(1): e1-e6, 2019 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30600282
12.
Cytogenetic abnormalities predict survival after allogeneic hematopoietic stem cell transplantation for pediatric acute myeloid leukemia: a PDWP/EBMT study.
Bone Marrow Transplant
; 59(4): 451-458, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-38225386
13.
Hematopoietic cell transplantation and gene therapy for Diamond-Blackfan anemia: state of the art and science.
Front Oncol
; 13: 1236038, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37752993
14.
An RPS19-edited model for Diamond-Blackfan anemia reveals TP53-dependent impairment of hematopoietic stem cell activity.
JCI Insight
; 8(1)2023 01 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-36413407
15.
Ex vivo prime editing of patient haematopoietic stem cells rescues sickle-cell disease phenotypes after engraftment in mice.
Nat Biomed Eng
; 7(5): 616-628, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-37069266
16.
Potent and uniform fetal hemoglobin induction via base editing.
Nat Genet
; 55(7): 1210-1220, 2023 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-37400614
17.
Case 3: Increased Snoring in a 7-year-old Boy.
Pediatr Rev
; 38(12): 569, 2017 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-29196514
18.
Case 2: Hypotonia and Muscle Weakness since Birth in a 2-year-old Boy.
Pediatr Rev
; 38(11): 531, 2017 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-29093122
19.
Erythropoietin regulation of red blood cell production: from bench to bedside and back.
F1000Res
; 92020.
Artigo
em Inglês
| MEDLINE | ID: mdl-32983414
20.
Pharmacokinetics of alemtuzumab in pediatric patients undergoing ex vivo T-cell-depleted haploidentical hematopoietic cell transplantation.
Cancer Chemother Pharmacol
; 86(6): 711-717, 2020 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-33037919