Detalhe da pesquisa
1.
Genomic signature of Fanconi anaemia DNA repair pathway deficiency in cancer.
Nature
; 612(7940): 495-502, 2022 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-36450981
2.
CRISPR-Cas9 Editing of the HBG1 and HBG2 Promoters to Treat Sickle Cell Disease.
N Engl J Med
; 389(9): 820-832, 2023 Aug 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-37646679
3.
Impact of rabbit anti-thymocyte globulin (ATG) exposure on outcomes after ex vivo T-cell-depleted hematopoietic cell transplantation in pediatric and young adult patients.
Cytotherapy
; 26(4): 351-359, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-38349310
4.
Two novel assays demonstrate persistent daratumumab exposure in a pediatric patient with delayed engraftment following allogeneic hematopoietic stem cell transplantation.
Cytotherapy
; 26(5): 466-471, 2024 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-38430078
5.
CD4+ T-cell reconstitution predicts survival outcomes after acute graft-versus-host-disease: a dual-center validation.
Blood
; 137(6): 848-855, 2021 02 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33150379
6.
Time to initiation of pre-emptive therapy for cytomegalovirus impacts overall survival in pediatric hematopoietic stem cell transplant recipients.
Cytotherapy
; 24(4): 428-436, 2022 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-35042670
7.
Toxicity and response after CD19-specific CAR T-cell therapy in pediatric/young adult relapsed/refractory B-ALL.
Blood
; 134(26): 2361-2368, 2019 12 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-31650176
8.
Emerging trends in COVID-19 treatment: learning from inflammatory conditions associated with cellular therapies.
Cytotherapy
; 22(9): 474-481, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32565132
9.
Early CD4+ T cell reconstitution as predictor of outcomes after allogeneic hematopoietic cell transplantation.
Cytotherapy
; 22(9): 503-510, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32622752
10.
Donor-specific antibody desensitization with daratumumab prior to haematopoietic cell transplant for sickle cell disease: A case report.
Br J Haematol
; 204(4): 1540-1544, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-38212144
11.
Emapalumab as bridge to hematopoietic cell transplant for STAT1 gain-of-function mutations.
J Allergy Clin Immunol
; 152(3): 815-817, 2023 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-37367708
12.
Long-term safety and efficacy of factor IX gene therapy in hemophilia B.
N Engl J Med
; 371(21): 1994-2004, 2014 Nov 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-25409372
13.
The clinical severity of hemoglobin S/Black (A γδß)0 -thalassemia.
Pediatr Blood Cancer
; 64(11)2017 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-28453928
14.
Addressing challenges of clinical trials in acute pain: The Pain Management of Vaso-occlusive Crisis in Children and Young Adults with Sickle Cell Disease Study.
Clin Trials
; 13(4): 409-16, 2016 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-27000103
15.
Silent cerebral infarcts in very young children with sickle cell anaemia are associated with a higher risk of stroke.
Br J Haematol
; 171(1): 120-9, 2015 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-26058476
16.
Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant.
Blood
; 121(17): 3335-44, 2013 Apr 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-23426947
17.
Retrospective Evaluation of Cystatin C as a Measure of Renal Function in Pediatric Hematopoietic Stem Cell Transplant Patients Receiving Foscarnet for Cytomegalovirus Reactivation.
Pediatr Infect Dis J
; 43(5): 457-462, 2024 May 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-38190640
18.
Predictors of outcomes in hematopoietic cell transplantation for Fanconi anemia.
Bone Marrow Transplant
; 59(1): 34-40, 2024 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-37848556
19.
Persistent or New Cytopenias Predict Relapse Better than Routine Bone Marrow Aspirate Evaluations After Hematopoietic Cell Transplantation for Acute Leukemia or Myelodysplastic Syndrome in Children and Young Adult Patients.
Transplant Cell Ther
; 2024 Apr 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-38643958
20.
T-cell depleted allogeneic hematopoietic stem cell transplant for the treatment of Fanconi anemia and MDS/AML.
Bone Marrow Transplant
; 59(1): 23-33, 2024 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-37773270