Detalhe da pesquisa
1.
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.
Sci Transl Med
; 16(733): eadh8162, 2024 Feb 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-38324638
2.
Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations.
Front Immunol
; 14: 1268620, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-38022635