Detalhe da pesquisa
1.
Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.
Blood
; 115(23): 4678-88, 2010 Jun 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-20335222
2.
Efficacy and safety of long-term prophylaxis in severe hemophilia A dogs following liver gene therapy using AAV vectors.
Mol Ther
; 19(3): 442-9, 2011 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-21081906
3.
Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B.
Mol Ther
; 18(11): 1896-906, 2010 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-20717103
4.
Safety of AAV factor IX peripheral transvenular gene delivery to muscle in hemophilia B dogs.
Mol Ther
; 18(7): 1318-29, 2010 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-20424599