Detalhe da pesquisa
1.
Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria.
N Engl J Med
; 390(11): 994-1008, 2024 Mar 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-38477987
2.
Eltrombopag Added to Immunosuppression in Severe Aplastic Anemia.
N Engl J Med
; 386(1): 11-23, 2022 01 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-34986284
3.
Rare germline complement factor H variants in patients with paroxysmal nocturnal hemoglobinuria.
Blood
; 141(15): 1812-1816, 2023 04 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-36626252
4.
The clinical picture of ERCC6L2 disease: from bone marrow failure to acute leukemia.
Blood
; 141(23): 2853-2866, 2023 06 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-36952636
5.
Liver disease in germline mutations of telomere-related genes: Prevalence, clinical, radiological, pathological features, outcome, and risk factors.
Hepatology
; 2023 Nov 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-37934624
6.
Clinical and immune features of human parvovirus B19 infection in allogeneic stem cell transplantation recipients: A retrospective monocentric study.
Transpl Infect Dis
; 25(5): e14118, 2023 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-37594199
7.
Determinants of survival after lung transplantation in telomerase-related gene mutation carriers: A retrospective cohort.
Am J Transplant
; 22(4): 1236-1244, 2022 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-34854205
8.
The complement C5 inhibitor crovalimab in paroxysmal nocturnal hemoglobinuria.
Blood
; 135(12): 912-920, 2020 03 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-31978221
9.
Emerging drugs for the treatment of paroxysmal nocturnal hemoglobinuria.
Expert Opin Emerg Drugs
; 27(1): 33-43, 2022 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-35078384
10.
The burden of illness of patients with paroxysmal nocturnal haemoglobinuria receiving C5 inhibitors in France, Germany and the United Kingdom: Patient-reported insights on symptoms and quality of life.
Eur J Haematol
; 109(4): 351-363, 2022 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-35746830
11.
Treatment for pure red cell aplasia after major ABO-incompatible allogeneic stem cell transplantation: a multicentre study.
Br J Haematol
; 193(4): 814-826, 2021 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-33844842
12.
Recurrent bacterial infections, but not fungal infections, characterise patients with ELANE-related neutropenia: a French Severe Chronic Neutropenia Registry study.
Br J Haematol
; 194(5): 908-920, 2021 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-34340247
13.
Ravulizumab (ALXN1210) vs eculizumab in adult patients with PNH naive to complement inhibitors: the 301 study.
Blood
; 133(6): 530-539, 2019 02 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30510080
14.
Germline DDX41 mutations define a significant entity within adult MDS/AML patients.
Blood
; 134(17): 1441-1444, 2019 10 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-31484648
15.
Elastography improves accuracy of early hepato-biliary complications diagnosis after allogeneic stem cell transplantation.
Haematologica
; 106(9): 2374-2383, 2021 09 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-32732366
16.
Effect of Ruxolitinib on Lung Function after Allogeneic Stem Cell Transplantation.
Biol Blood Marrow Transplant
; 26(11): 2115-2120, 2020 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-32738501
17.
Letermovir for Secondary Prophylaxis of Cytomegalovirus Infection and Disease after Allogeneic Hematopoietic Cell Transplantation: Results from the French Compassionate Program.
Biol Blood Marrow Transplant
; 26(5): 978-984, 2020 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-32035273
18.
Human-Derived α1-Antitrypsin is Still Efficacious in Heavily Pretreated Patients with Steroid-Resistant Gastrointestinal Graft-versus-Host Disease.
Biol Blood Marrow Transplant
; 26(9): 1620-1626, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32454215
19.
IPSS-M in myelodysplastic neoplasms arising from aplastic anemia and paroxysmal nocturnal hemoglobinuria.
Blood
; 141(25): 3122-3125, 2023 06 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-37053552
20.
Unrelated cord blood transplantation in patients with idiopathic refractory severe aplastic anemia: a nationwide phase 2 study.
Blood
; 132(7): 750-754, 2018 08 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-29760162