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The nucleoside analog clitocine is a potent and efficacious readthrough agent.
Friesen, Westley J; Trotta, Christopher R; Tomizawa, Yuki; Zhuo, Jin; Johnson, Briana; Sierra, Jairo; Roy, Bijoyita; Weetall, Marla; Hedrick, Jean; Sheedy, Josephine; Takasugi, James; Moon, Young-Choon; Babu, Suresh; Baiazitov, Ramil; Leszyk, John D; Davis, Thomas W; Colacino, Joseph M; Peltz, Stuart W; Welch, Ellen M.
Affiliation
  • Friesen WJ; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA wfriesen@ptcbio.com.
  • Trotta CR; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Tomizawa Y; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Zhuo J; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Johnson B; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Sierra J; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Roy B; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Weetall M; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Hedrick J; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Sheedy J; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Takasugi J; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Moon YC; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Babu S; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Baiazitov R; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Leszyk JD; Department of Biochemistry and Molecular Pharmacology, University of Massachusetts Medical School, Worcester, Massachusetts 01655-0122, USA.
  • Davis TW; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Colacino JM; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Peltz SW; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
  • Welch EM; PTC Therapeutics, Inc., South Plainfield, New Jersey 07080, USA.
RNA ; 23(4): 567-577, 2017 04.
Article in En | MEDLINE | ID: mdl-28096517

Full text: 1 Database: MEDLINE Main subject: Ovarian Neoplasms / Pyrimidine Nucleosides / Tumor Suppressor Protein p53 / Codon, Nonsense / Biomimetic Materials / Furans / Antimetabolites, Antineoplastic / Nucleosides Limits: Animals / Female / Humans Language: En Journal: RNA Journal subject: BIOLOGIA MOLECULAR Year: 2017 Type: Article Affiliation country: United States

Full text: 1 Database: MEDLINE Main subject: Ovarian Neoplasms / Pyrimidine Nucleosides / Tumor Suppressor Protein p53 / Codon, Nonsense / Biomimetic Materials / Furans / Antimetabolites, Antineoplastic / Nucleosides Limits: Animals / Female / Humans Language: En Journal: RNA Journal subject: BIOLOGIA MOLECULAR Year: 2017 Type: Article Affiliation country: United States