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Towards personalised allele-specific CRISPR gene editing to treat autosomal dominant disorders.
Christie, Kathleen A; Courtney, David G; DeDionisio, Larry A; Shern, Connie Chao; De Majumdar, Shyamasree; Mairs, Laura C; Nesbit, M Andrew; Moore, C B Tara.
Affiliation
  • Christie KA; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK.
  • Courtney DG; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK.
  • DeDionisio LA; Avellino Laboratories, Menlo Park, California, CA, 94025, USA.
  • Shern CC; Avellino Laboratories, Menlo Park, California, CA, 94025, USA.
  • De Majumdar S; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK.
  • Mairs LC; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK.
  • Nesbit MA; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK.
  • Moore CBT; Biomedical Sciences Research Institute, Ulster University, Coleraine, Northern Ireland, BT52 1SA, UK. t.moore@ulster.ac.uk.
Sci Rep ; 7(1): 16174, 2017 11 23.
Article in En | MEDLINE | ID: mdl-29170458

Full text: 1 Database: MEDLINE Main subject: Clustered Regularly Interspaced Short Palindromic Repeats / Gene Editing Limits: Animals Language: En Journal: Sci Rep Year: 2017 Type: Article Affiliation country: United kingdom

Full text: 1 Database: MEDLINE Main subject: Clustered Regularly Interspaced Short Palindromic Repeats / Gene Editing Limits: Animals Language: En Journal: Sci Rep Year: 2017 Type: Article Affiliation country: United kingdom