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High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation.
Magis, Wendy; DeWitt, Mark A; Wyman, Stacia K; Vu, Jonathan T; Heo, Seok-Jin; Shao, Shirley J; Hennig, Finn; Romero, Zulema G; Campo-Fernandez, Beatriz; Said, Suzanne; McNeill, Matthew S; Rettig, Garrett R; Sun, Yongming; Wang, Yu; Behlke, Mark A; Kohn, Donald B; Boffelli, Dario; Walters, Mark C; Corn, Jacob E; Martin, David I K.
Affiliation
  • Magis W; Children's Hospital Oakland Research Institute, UCSF Benioff Children's Hospital Oakland, Oakland, CA 94609, USA.
  • DeWitt MA; Innovative Genomics Institute, University of California, Berkeley, CA 94720, USA.
  • Wyman SK; Innovative Genomics Institute, University of California, Berkeley, CA 94720, USA.
  • Vu JT; Innovative Genomics Institute, University of California, Berkeley, CA 94720, USA.
  • Heo SJ; Children's Hospital Oakland Research Institute, UCSF Benioff Children's Hospital Oakland, Oakland, CA 94609, USA.
  • Shao SJ; Innovative Genomics Institute, University of California, Berkeley, CA 94720, USA.
  • Hennig F; Jacob's School of Medicine and Biomedical Sciences, Buffalo, NY 14203, USA.
  • Romero ZG; Departments of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, CA 90095, USA.
  • Campo-Fernandez B; Departments of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, CA 90095, USA.
  • Said S; Departments of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, CA 90095, USA.
  • McNeill MS; Integrated DNA Technologies, Coralville, IA 52241, USA.
  • Rettig GR; Integrated DNA Technologies, Coralville, IA 52241, USA.
  • Sun Y; Integrated DNA Technologies, Redwood City, CA 94065, USA.
  • Wang Y; Integrated DNA Technologies, Redwood City, CA 94065, USA.
  • Behlke MA; Integrated DNA Technologies, Coralville, IA 52241, USA.
  • Kohn DB; Departments of Microbiology, Immunology, and Molecular Genetics, University of California, Los Angeles, CA 90095, USA.
  • Boffelli D; Children's Hospital Oakland Research Institute, UCSF Benioff Children's Hospital Oakland, Oakland, CA 94609, USA.
  • Walters MC; Children's Hospital Oakland Research Institute, UCSF Benioff Children's Hospital Oakland, Oakland, CA 94609, USA.
  • Corn JE; Blood and Marrow Transplant Program, Division of Hematology, UCSF Benioff Children's Hospital Oakland, Oakland, CA 94609, USA.
  • Martin DIK; Innovative Genomics Institute, University of California, Berkeley, CA 94720, USA.
iScience ; 25(6): 104374, 2022 Jun 17.
Article in En | MEDLINE | ID: mdl-35633935

Full text: 1 Database: MEDLINE Type of study: Guideline Language: En Journal: IScience Year: 2022 Type: Article Affiliation country: United States

Full text: 1 Database: MEDLINE Type of study: Guideline Language: En Journal: IScience Year: 2022 Type: Article Affiliation country: United States