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Nusinersen in adult patients with 5q spinal muscular atrophy: A multicenter observational cohorts' study.
Vázquez-Costa, Juan F; Povedano, Mónica; Nascimiento-Osorio, Andrés E; Moreno Escribano, Antonio; Kapetanovic Garcia, Solange; Dominguez, Raul; Exposito, Jessica M; González, Laura; Marco, Carla; Medina Castillo, Julita; Muelas, Nuria; Natera de Benito, Daniel; Ñungo Garzón, Nancy Carolina; Pitarch Castellano, Inmaculada; Sevilla, Teresa; Hervás, David.
Affiliation
  • Vázquez-Costa JF; Neuromuscular Unit, Department of Neurology, Hospital Universitario y Politécnico la Fe, Valencia, Spain.
  • Povedano M; Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Valencia, Spain.
  • Nascimiento-Osorio AE; Department of Medicine, Universitat de València, Valencia, Spain.
  • Moreno Escribano A; Motor Neuron Unit, Neurology Department, Bellvitge Hospital-IDIBELL, Barcelona, Spain.
  • Kapetanovic Garcia S; Neuromuscular Unit, Neuropediatric Department, Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Barcelona, Spain.
  • Dominguez R; Center for the Biomedical Research on Rare Diseases (CIBERER), ISCIII, Madrid, Spain.
  • Exposito JM; Neuromuscular Unit, Neurology Department, Hospital Clínico Universitario Virgen de la Arrixaca, Murcia, Spain.
  • González L; ALS and Neuromuscular Unit, Neurology Department, Hospital Universitario Basurto-OSI Bilbao, Bilbao, Spain.
  • Marco C; Motor Neuron Unit, Neurology Department, Bellvitge Hospital-IDIBELL, Barcelona, Spain.
  • Medina Castillo J; Neuromuscular Unit, Neuropediatric Department, Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Barcelona, Spain.
  • Muelas N; Motor Neuron Unit, Neurology Department, Bellvitge Hospital-IDIBELL, Barcelona, Spain.
  • Natera de Benito D; Motor Neuron Unit, Neurology Department, Bellvitge Hospital-IDIBELL, Barcelona, Spain.
  • Ñungo Garzón NC; Physical Medicine and Rehabilitation Department, Hospital Sant Joan de Deu, Barcelona, Spain.
  • Pitarch Castellano I; Neuromuscular Unit, Department of Neurology, Hospital Universitario y Politécnico la Fe, Valencia, Spain.
  • Sevilla T; Centro de Investigación Biomédica en Red de Enfermedades Raras (CIBERER), Valencia, Spain.
  • Hervás D; Neuromuscular Unit, Neuropediatric Department, Institut de Recerca Pediàtrica Hospital Sant Joan de Déu, Barcelona, Spain.
Eur J Neurol ; 29(11): 3337-3346, 2022 11.
Article in En | MEDLINE | ID: mdl-35872571

Full text: 1 Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Type of study: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adult / Humans Language: En Journal: Eur J Neurol Journal subject: NEUROLOGIA Year: 2022 Type: Article Affiliation country: Spain

Full text: 1 Database: MEDLINE Main subject: Muscular Atrophy, Spinal / Spinal Muscular Atrophies of Childhood Type of study: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limits: Adult / Humans Language: En Journal: Eur J Neurol Journal subject: NEUROLOGIA Year: 2022 Type: Article Affiliation country: Spain