Adenine base editor-mediated correction of the common and severe IVS1-110 (G>A) ß-thalassemia mutation.
Blood
; 141(10): 1169-1179, 2023 03 09.
Article
in En
| MEDLINE
| ID: mdl-36508706
Full text:
1
Database:
MEDLINE
Main subject:
Beta-Thalassemia
Limits:
Humans
Language:
En
Journal:
Blood
Year:
2023
Type:
Article
Affiliation country:
France