Rescue of blood coagulation Factor VIII exon-16 mis-splicing by antisense oligonucleotides.

Tse, Victor; Chacaltana, Guillermo; Gutierrez, Martin; Forino, Nicholas M; Jimenez, Arcelia G; Tao, Hanzhang; Do, Phong H; Oh, Catherine; Chary, Priyanka; Quesada, Isabel; Hamrick, Antonia; Lee, Sophie; Stone, Michael D; Sanford, Jeremy R.

bioRxiv ; 2023 Apr 01.

Article in En | MEDLINE | ID: mdl-37034721

Full text: 1 Database: MEDLINE Type of study: Prognostic_studies Language: En Journal: BioRxiv Year: 2023 Type: Article

Full text: 1 Database: MEDLINE Type of study: Prognostic_studies Language: En Journal: BioRxiv Year: 2023 Type: Article