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Neurodegeneration in patients with multisystem Langerhans cell histiocytosis treated with vemurafenib.
Trambusti, Irene; Pegoraro, Francesco; Gaspari, Stefania; Dell'Acqua, Fabiola; Cellini, Monica; Trizzino, Antonino; Tondo, Annalisa; Perrone, Anna; Coniglio, Maria Luisa; Guerrini, Renzo; Barba, Carmen; Sieni, Elena.
Affiliation
  • Trambusti I; Pediatric Hematology-Oncology Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Pegoraro F; Pediatric Hematology-Oncology Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Gaspari S; Department of Experimental and Clinical Medicine, University of Florence, Florence, Italy.
  • Dell'Acqua F; Pediatric Hematology/Oncology Department, Cell and Gene Therapy, Scientific Institute for Research, IRCCS Bambino Gesù Children's Hospital, Rome, Italy.
  • Cellini M; Pediatric Hematology-Oncology Department, Fondazione IRCCS San Gerardo dei Tintori, Monza, Italy.
  • Trizzino A; Pediatric Hematology Oncology Department, Azienda Ospedaliero Universitaria Policlinico di Modena, Modena, Italy.
  • Tondo A; Pediatric Hemato-Oncology Department, ARNAS Ospedali Civico, G. Di Cristina, Palermo, Italy.
  • Perrone A; Pediatric Hematology-Oncology Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Coniglio ML; Pediatric Radiology Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Guerrini R; Pediatric Hematology-Oncology Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Barba C; Neuroscience Department, Meyer Children's Hospital IRCCS, Florence, Italy.
  • Sieni E; Department of Neurosciences, Psychology, Drug Research and Child Health, University of Florence, Florence, Italy.
Br J Haematol ; 204(6): 2508-2511, 2024 Jun.
Article in En | MEDLINE | ID: mdl-38665038

Full text: 1 Database: MEDLINE Main subject: Histiocytosis, Langerhans-Cell / Vemurafenib Limits: Adult / Child / Female / Humans / Male / Middle aged Language: En Journal: Br J Haematol Year: 2024 Type: Article Affiliation country: Italy

Full text: 1 Database: MEDLINE Main subject: Histiocytosis, Langerhans-Cell / Vemurafenib Limits: Adult / Child / Female / Humans / Male / Middle aged Language: En Journal: Br J Haematol Year: 2024 Type: Article Affiliation country: Italy