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miRNA-embedded shRNAs for Lineage-specific BCL11A Knockdown and Hemoglobin F Induction.
Guda, Swaroopa; Brendel, Christian; Renella, Raffaele; Du, Peng; Bauer, Daniel E; Canver, Matthew C; Grenier, Jennifer K; Grimson, Andrew W; Kamran, Sophia C; Thornton, James; de Boer, Helen; Root, David E; Milsom, Michael D; Orkin, Stuart H; Gregory, Richard I; Williams, David A.
Afiliación
  • Guda S; Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • Brendel C; Harvard Medical School, Boston, Massachusetts, USA.
  • Renella R; Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • Du P; Harvard Medical School, Boston, Massachusetts, USA.
  • Bauer DE; Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • Canver MC; Harvard Medical School, Boston, Massachusetts, USA.
  • Grenier JK; Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts, USA.
  • Grimson AW; Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • Kamran SC; Stem Cell Program, Boston Children's Hospital, Department of Biological Chemistry and Molecular Pharmacology, Harvard Medical School, Harvard Stem Cell Institute, Boston, Massachusetts, USA.
  • Thornton J; Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts, USA.
  • de Boer H; Harvard Medical School, Boston, Massachusetts, USA.
  • Root DE; Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts, USA.
  • Milsom MD; Harvard Medical School, Boston, Massachusetts, USA.
  • Orkin SH; Genetic Perturbation Platform, Broad Institute of Harvard and MIT, Cambridge, Massachusetts, USA.
  • Gregory RI; Department of Molecular Biology & Genetics, College of Arts and Sciences, Cornell University, Ithaca, New York, USA.
  • Williams DA; Harvard Medical School, Boston, Massachusetts, USA.
Mol Ther ; 23(9): 1465-74, 2015 Sep.
Article en En | MEDLINE | ID: mdl-26080908

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Hemoglobina Fetal / Linaje de la Célula / Silenciador del Gen / MicroARNs / ARN Interferente Pequeño / Interferencia de ARN Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2015 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Hemoglobina Fetal / Linaje de la Célula / Silenciador del Gen / MicroARNs / ARN Interferente Pequeño / Interferencia de ARN Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2015 Tipo del documento: Article País de afiliación: Estados Unidos