Your browser doesn't support javascript.
loading
COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa.
Hainzl, Stefan; Peking, Patricia; Kocher, Thomas; Murauer, Eva M; Larcher, Fernando; Del Rio, Marcela; Duarte, Blanca; Steiner, Markus; Klausegger, Alfred; Bauer, Johann W; Reichelt, Julia; Koller, Ulrich.
Afiliación
  • Hainzl S; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Peking P; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Kocher T; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Murauer EM; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Larcher F; Epithelial Biomedicine Division, CIEMAT-CIBERER, Department of Bioengineering, UC3M, Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, 28040 Madrid, Spain.
  • Del Rio M; Epithelial Biomedicine Division, CIEMAT-CIBERER, Department of Bioengineering, UC3M, Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, 28040 Madrid, Spain.
  • Duarte B; Epithelial Biomedicine Division, CIEMAT-CIBERER, Department of Bioengineering, UC3M, Instituto de Investigación Sanitaria de la Fundación Jiménez Díaz, 28040 Madrid, Spain.
  • Steiner M; Laboratory for Immunological and Molecular Cancer Research, 3rd Medical Department with Hematology, Medical Oncology, Hemostaseology, Infectious Diseases and Rheumatology, Oncologic Center, Paracelsus Medical University, 5020 Salzburg, Austria.
  • Klausegger A; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Bauer JW; Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Reichelt J; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria.
  • Koller U; EB House Austria, Research Program for Molecular Therapy of Genodermatoses, Department of Dermatology, University Hospital of the Paracelsus Medical University, 5020 Salzburg, Austria. Electronic address: u.koller@salk.at.
Mol Ther ; 25(11): 2573-2584, 2017 11 01.
Article en En | MEDLINE | ID: mdl-28800953

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Queratinocitos / Epidermólisis Ampollosa Distrófica / Colágeno Tipo VII / Terapia Molecular Dirigida / Sistemas CRISPR-Cas / Edición Génica Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2017 Tipo del documento: Article País de afiliación: Austria

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Queratinocitos / Epidermólisis Ampollosa Distrófica / Colágeno Tipo VII / Terapia Molecular Dirigida / Sistemas CRISPR-Cas / Edición Génica Tipo de estudio: Prognostic_studies Límite: Animals / Humans Idioma: En Revista: Mol Ther Asunto de la revista: BIOLOGIA MOLECULAR / TERAPEUTICA Año: 2017 Tipo del documento: Article País de afiliación: Austria