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Effective hematopoietic stem cell-based gene therapy in a murine model of hereditary pulmonary alveolar proteinosis.
Hetzel, Miriam; Lopez-Rodriguez, Elena; Mucci, Adele; Nguyen, Ariane Hai Ha; Suzuki, Takuji; Shima, Kenjiro; Buchegger, Theresa; Dettmer, Sabine; Rodt, Thomas; Bankstahl, Jens P; Malik, Punam; Knudsen, Lars; Schambach, Axel; Hansen, Gesine; Trapnell, Bruce C; Lachmann, Nico; Moritz, Thomas.
Afiliación
  • Hetzel M; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Lopez-Rodriguez E; Institute of Functional and Applied Anatomy, Hannover Medical School, Hannover, Germany.
  • Mucci A; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Nguyen AHH; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Suzuki T; Translational Pulmonary Science Center, Division of Pulmonary Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Shima K; Division of Pulmonary Medicine, Jichi Medical University, Shimotsukeshi, Tochigi, Japan.
  • Buchegger T; Translational Pulmonary Science Center, Division of Pulmonary Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Dettmer S; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Rodt T; Department of Radiology, Hannover Medical School, Hannover, Germany.
  • Bankstahl JP; Department of Radiology, Hannover Medical School, Hannover, Germany.
  • Malik P; Department of Nuclear Medicine, Hannover Medical School, Hannover, Germany.
  • Knudsen L; Division of Experimental Hematology and Cancer Biology, Cancer and Blood Disease Institute (CBDI), Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Schambach A; Institute of Functional and Applied Anatomy, Hannover Medical School, Hannover, Germany.
  • Hansen G; Institute of Experimental Hematology, Hannover Medical School, Hannover, Germany.
  • Trapnell BC; Division of Hematology/Oncology, Boston Children's Hospital, Harvard Medical School, Boston, MA, USA.
  • Lachmann N; Department of Pediatrics, Allergology, and Neonatology, Hannover Medical School, Hannover, Germany.
  • Moritz T; Translational Pulmonary Science Center, Division of Pulmonary Biology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
Haematologica ; 105(4): 1147-1157, 2020 04.
Article en En | MEDLINE | ID: mdl-31289207

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Proteinosis Alveolar Pulmonar Límite: Animals Idioma: En Revista: Haematologica Año: 2020 Tipo del documento: Article País de afiliación: Alemania

Texto completo: 1 Bases de datos: MEDLINE Asunto principal: Proteinosis Alveolar Pulmonar Límite: Animals Idioma: En Revista: Haematologica Año: 2020 Tipo del documento: Article País de afiliación: Alemania